Nusinersen in type 1 spinal muscular atrophy: Twelve‐month real‐world data
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Title
Nusinersen in type 1 spinal muscular atrophy: Twelve‐month real‐world data
Authors
Keywords
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Journal
ANNALS OF NEUROLOGY
Volume -, Issue -, Pages -
Publisher
Wiley
Online
2019-06-22
DOI
10.1002/ana.25533
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- 209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7–9 November 2014, Heemskerk, The Netherlands
- (2015) Richard Finkel et al. NEUROMUSCULAR DISORDERS
- Observational study of spinal muscular atrophy type I and implications for clinical trials
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- SMA-EUROPE workshop report: opportunities and challenges in developing clinical trials for spinal muscular atrophy in Europe
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