Editing the Sickle Cell Disease Mutation in Primary Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates

Published 2019 View Full Article

Authors

Keywords

hematopoietic stem cells, sickle cell disease, gene editing, homologous recombination, non-homologous end joining, CRISPR/Cas9, zinc finger nuclease, adeno-associated virus 6

Journal

MOLECULAR THERAPY

Volume -, Issue -, Pages -

Publisher

Elsevier BV

Online

2019-05-24

DOI

10.1016/j.ymthe.2019.05.014

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