CRISPR-Cas9 corrects Duchenne muscular dystrophy exon 44 deletion mutations in mice and human cells
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Title
CRISPR-Cas9 corrects Duchenne muscular dystrophy exon 44 deletion mutations in mice and human cells
Authors
Keywords
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Journal
Science Advances
Volume 5, Issue 3, Pages eaav4324
Publisher
American Association for the Advancement of Science (AAAS)
Online
2019-03-07
DOI
10.1126/sciadv.aav4324
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