Design of Potent Mannose 6-Phosphate Analogues for the Functionalization of Lysosomal Enzymes To Improve the Treatment of Pompe Disease

Mannose-6-Phosphate Receptor: A Target for Theranostics of Prostate Cancer

(2015) Ophélie Vaillant et al.   ANGEWANDTE CHEMIE-INTERNATIONAL EDITION

Treatment of lysosomal storage disorders: successes and challenges

(2014) Carla E. M. Hollak et al.   JOURNAL OF INHERITED METABOLIC DISEASE

Comparative study on mannose 6-phosphate residue contents of recombinant lysosomal enzymes

(2014) Tadayasu Togawa et al.   MOLECULAR GENETICS AND METABOLISM

Glycosylation-independent Lysosomal Targeting of Acid α-Glucosidase Enhances Muscle Glycogen Clearance in Pompe Mice

(2012) John A. Maga et al.   JOURNAL OF BIOLOGICAL CHEMISTRY

Enzyme replacement therapy in late-onset Pompe disease: a systematic literature review

(2012) Antonio Toscano et al.   JOURNAL OF NEUROLOGY

Carbohydrate recognition by the mannose-6-phosphate receptors

(2009) Jung-Ja P Kim et al.   CURRENT OPINION IN STRUCTURAL BIOLOGY

Glycoengineered Acid α-Glucosidase With Improved Efficacy at Correcting the Metabolic Aberrations and Motor Function Deficits in a Mouse Model of Pompe Disease

(2009) Yunxiang Zhu et al.   MOLECULAR THERAPY

Hydrolytic Stability of Hydrazones and Oximes

(2008) Jeet Kalia et al.   ANGEWANDTE CHEMIE-INTERNATIONAL EDITION

Synthesis of new sulfonate and phosphonate derivatives for cation-independent mannose 6-phosphate receptor targeting

(2008) Audrey Jeanjean et al.   BIOORGANIC & MEDICINAL CHEMISTRY LETTERS

Pompe's disease

(2008) Ans T van der Ploeg et al.   LANCET

Biochemical and pharmacological characterization of different recombinant acid α-glucosidase preparations evaluated for the treatment of Pompe disease

(2008) A.J. McVie-Wylie et al.   MOLECULAR GENETICS AND METABOLISM