Phase I clinical evaluation of CNSA-001 (sepiapterin), a novel pharmacological treatment for phenylketonuria and tetrahydrobiopterin deficiencies, in healthy volunteers

Title
Phase I clinical evaluation of CNSA-001 (sepiapterin), a novel pharmacological treatment for phenylketonuria and tetrahydrobiopterin deficiencies, in healthy volunteers
Authors
Keywords
CNSA-001, Sepiapterin, tetrahydrobiopterin, BH, 4, , Phenylketonuria, PKU, Primary BH, 4, deficiency
Journal
MOLECULAR GENETICS AND METABOLISM
Volume -, Issue -, Pages -
Publisher
Elsevier BV
Online
2019-02-11
DOI
10.1016/j.ymgme.2019.02.001

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