In vivo hematopoietic stem cell gene therapy ameliorates murine thalassemia intermedia
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Title
In vivo hematopoietic stem cell gene therapy ameliorates murine thalassemia intermedia
Authors
Keywords
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Journal
JOURNAL OF CLINICAL INVESTIGATION
Volume -, Issue -, Pages -
Publisher
American Society for Clinical Investigation
Online
2018-11-14
DOI
10.1172/jci122836
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