Recent advances in the treatment of familial amyloid polyneuropathy

Doxycycline plus tauroursodeoxycholic acid for transthyretin amyloidosis: a phase II study

(2012) Laura Obici et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Regional difference and similarity of familial amyloidosis with polyneuropathy in France

(2012) David Adams et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Clinical development of an antisense therapy for the treatment of transthyretin-associated polyneuropathy

(2012) Elizabeth J. Ackermann et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Transthyretin Amyloidosis and the Kidney

(2012) L. Lobato et al.   Clinical Journal of the American Society of Nephrology

Amyloid neuropathies

(2012) David Adams et al.   CURRENT OPINION IN NEUROLOGY

The Transthyretin Amyloidoses: From Delineating the Molecular Mechanism of Aggregation Linked to Pathology to a Regulatory-Agency-Approved Drug

(2012) Steven M. Johnson et al.   JOURNAL OF MOLECULAR BIOLOGY

Natural history of transthyretin Val30Met familial amyloid polyneuropathy: analysis of late-onset cases from non-endemic areas

(2012) Haruki Koike et al.   JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY

Tafamidis for transthyretin familial amyloid polyneuropathy: A randomized, controlled trial

(2012) T. Coelho et al.   NEUROLOGY

Long-term survival after liver transplantation in patients with familial amyloid polyneuropathy

(2012) T. Yamashita et al.   NEUROLOGY

Symptomatic and provende novoamyloid polyneuropathy in familial amyloid polyneuropathy domino liver recipients

(2011) D. Adams et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Long-term data from the Familial Amyloidotic Polyneuropathy World Transplant Registry (FAPWTR)

(2011) H. E. Wilczek et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

The diflunisal trial: update on study drug tolerance and disease progression

(2011) J. L. Berk et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Characterization of End-Stage Renal Disease After Liver Transplantation in Transthyretin Amyloidosis (ATTR V30M)

(2011) A. Rocha et al.   TRANSPLANTATION PROCEEDINGS

Combined Heart and Kidney Transplantation Provides an Excellent Survival and Decreases Risk of Cardiac Cellular Rejection and Coronary Allograft Vasculopathy

(2011) E. Raichlin et al.   TRANSPLANTATION PROCEEDINGS

Suppression of choroid plexus transthyretin levels by antisense oligonucleotide treatment

(2010) Merrill D. Benson et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Biochemical effect of liver transplantation in two Swedish patients with familial amyloidotic polyneuropathy (FAP-met30)

(2010) Gösta Holmgren et al.   CLINICAL GENETICS

Synergy of combined Doxycycline/TUDCA treatment in lowering Transthyretin deposition and associated biomarkers: studies in FAP mouse models

(2010) Isabel Cardoso et al.   Journal of Translational Medicine

Risk of transmission of systemic transthyretin amyloidosis after domino liver transplantation

(2010) Laura Lladó et al.   LIVER TRANSPLANTATION

Acquired amyloid neuropathy in a Portuguese patient after domino liver transplantation

(2010) Isabel Conceição et al.   MUSCLE & NERVE

Antibodies to human serum amyloid P component eliminate visceral amyloid deposits

(2010) Karl Bodin et al.   NATURE

Progression of transthyretin amyloid neuropathy after liver transplantation

(2010) J. J. Liepnieks et al.   NEUROLOGY

Ocular manifestations in liver transplant recipients with familial amyloid polyneuropathy

(2008) Ola Sandgren et al.   ACTA OPHTHALMOLOGICA