Suppression of nonsense mutations as a therapeutic approach to treat genetic diseases
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Title
Suppression of nonsense mutations as a therapeutic approach to treat genetic diseases
Authors
Keywords
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Journal
Wiley Interdisciplinary Reviews-RNA
Volume 2, Issue 6, Pages 837-852
Publisher
Wiley
Online
2011-07-06
DOI
10.1002/wrna.95
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Note: Only part of the references are listed.- Chronic ataluren (PTC124) treatment of nonsense mutation cystic fibrosis
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