Exon-Skipping Antisense Oligonucleotides to Correct Missplicing in Neurogenetic Diseases

Title
Exon-Skipping Antisense Oligonucleotides to Correct Missplicing in Neurogenetic Diseases
Authors
Keywords
-
Journal
Nucleic Acid Therapeutics
Volume 24, Issue 1, Pages 69-86
Publisher
Mary Ann Liebert Inc
Online
2014-02-08
DOI
10.1089/nat.2013.0461

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