Evaluation of Aminoglycoside and Non-Aminoglycoside Compounds for Stop-Codon Readthrough Therapy in Four Lysosomal Storage Diseases
Published 2015 View Full Article
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Title
Evaluation of Aminoglycoside and Non-Aminoglycoside Compounds for Stop-Codon Readthrough Therapy in Four Lysosomal Storage Diseases
Authors
Keywords
Nonsense mutation, Fibroblasts, Lysosomes, Mutation, Point mutation, COS cells, Messenger RNA, Sulfates
Journal
PLoS One
Volume 10, Issue 8, Pages e0135873
Publisher
Public Library of Science (PLoS)
Online
2015-08-20
DOI
10.1371/journal.pone.0135873
References
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