Comparative Analysis of DNA Nanoparticles and AAVs for Ocular Gene Delivery
Published 2012 View Full Article
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Title
Comparative Analysis of DNA Nanoparticles and AAVs for Ocular Gene Delivery
Authors
Keywords
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Journal
PLoS One
Volume 7, Issue 12, Pages e52189
Publisher
Public Library of Science (PLoS)
Online
2012-12-19
DOI
10.1371/journal.pone.0052189
References
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- (2010) D. Amado et al. Science Translational Medicine
- Gene delivery to mitotic and postmitotic photoreceptors via compacted DNA nanoparticles results in improved phenotype in a mouse model of retinitis pigmentosa
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- Evidence for the Failure of Adeno-associated Virus Serotype 5 to Package a Viral Genome ≥8.2 kb
- (2009) Yi Lai et al. MOLECULAR THERAPY
- A Partial Structural and Functional Rescue of a Retinitis Pigmentosa Model with Compacted DNA Nanoparticles
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- Ocular Delivery of Compacted DNA-Nanoparticles Does Not Elicit Toxicity in the Mouse Retina
- (2009) Xi-Qin Ding et al. PLoS One
- AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects
- (2008) N C Hasbrouck et al. GENE THERAPY
- AAV-mediated gene therapy for retinal disorders: from mouse to man
- (2008) P K Buch et al. GENE THERAPY
- Stable Integration of Recombinant Adeno-Associated Virus Vector Genomes After Transduction of Murine Hematopoietic Stem Cells
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- Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial
- (2008) William W. Hauswirth et al. HUMAN GENE THERAPY
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- Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics
- (2008) A. V. Cideciyan et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Cell Surface Nucleolin Serves as Receptor for DNA Nanoparticles Composed of Pegylated Polylysine and DNA
- (2007) Xuguang Chen et al. MOLECULAR THERAPY
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