Modifications to toxic CUG RNAs induce structural stability, rescue mis-splicing in a myotonic dystrophy cell model and reduce toxicity in a myotonic dystrophy zebrafish model
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Title
Modifications to toxic CUG RNAs induce structural stability, rescue mis-splicing in a myotonic dystrophy cell model and reduce toxicity in a myotonic dystrophy zebrafish model
Authors
Keywords
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Journal
NUCLEIC ACIDS RESEARCH
Volume 42, Issue 20, Pages 12768-12778
Publisher
Oxford University Press (OUP)
Online
2014-10-11
DOI
10.1093/nar/gku941
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