Intracisternal enzyme replacement therapy in lysosomal storage diseases: dispersal pathways, regional enzyme concentrations and the effect of posttreatment posture

CNS Penetration of Intrathecal-Lumbar Idursulfase in the Monkey, Dog and Mouse: Implications for Neurological Outcomes of Lysosomal Storage Disorder

(2012) Pericles Calias et al.   PLoS One

Distribution of acid sphingomyelinase in rodent and non-human primate brain after intracerebroventricular infusion

(2011) Robin J. Ziegler et al.   EXPERIMENTAL NEUROLOGY

Treatment of canine fucosidosis by intracisternal enzyme infusion

(2011) Gauthami S. Kondagari et al.   EXPERIMENTAL NEUROLOGY

Intracerebroventricular enzyme infusion corrects central nervous system pathology and dysfunction in a mouse model of metachromatic leukodystrophy

(2011) S. Stroobants et al.   HUMAN MOLECULAR GENETICS

Therapeutic Potential of Intracerebroventricular Replacement of Modified Human β-Hexosaminidase B for GM2 Gangliosidosis

(2011) Kazuhiko Matsuoka et al.   MOLECULAR THERAPY

Enzyme replacement reduces neuropathology in MPS IIIA dogs

(2011) Allison C. Crawley et al.   NEUROBIOLOGY OF DISEASE

Highly phosphomannosylated enzyme replacement therapy for GM2 gangliosidosis

(2010) Daisuke Tsuji et al.   ANNALS OF NEUROLOGY

Recent insights into a new hydrodynamics of the cerebrospinal fluid

(2010) Marin Bulat et al.   BRAIN RESEARCH REVIEWS

SGSH gene transfer in mucopolysaccharidosis type IIIA mice using canine adenovirus vectors

(2010) Adeline A. Lau et al.   MOLECULAR GENETICS AND METABOLISM

Intracisternal enzyme replacement therapy in lysosomal storage diseases: routes of absorption into brain

(2010) R. D. Jolly et al.   NEUROPATHOLOGY AND APPLIED NEUROBIOLOGY

Effect of cisternal sulfamidase delivery in MPS IIIA Huntaway dogs—A proof of principle study

(2009) Kim M. Hemsley et al.   MOLECULAR GENETICS AND METABOLISM

Intrathecal administration of recombinant human N-acetylgalactosamine 4-sulfatase to a MPS VI patient with pachymeningitis cervicalis

(2009) María Verónica Muñoz-Rojas et al.   MOLECULAR GENETICS AND METABOLISM

Intrathecal enzyme replacement therapy in a patient with mucopolysaccharidosis type I and symptomatic spinal cord compression

(2008) Maria-Veronica Munoz-Rojas et al.   AMERICAN JOURNAL OF MEDICAL GENETICS PART A

Cerebrospinal fluid outflow: An evolving perspective

(2008) Kapil G. Kapoor et al.   BRAIN RESEARCH BULLETIN

Intracerebroventricular infusion of acid sphingomyelinase corrects CNS manifestations in a mouse model of Niemann–Pick A disease

(2008) James C. Dodge et al.   EXPERIMENTAL NEUROLOGY

Intraventricular Enzyme Replacement Improves Disease Phenotypes in a Mouse Model of Late Infantile Neuronal Ceroid Lipofuscinosis

(2008) Michael Chang et al.   MOLECULAR THERAPY

Solutes, but not cells, drain from the brain parenchyma along basement membranes of capillaries and arteries: significance for cerebral amyloid angiopathy and neuroimmunology

(2008) R. O. Carare et al.   NEUROPATHOLOGY AND APPLIED NEUROBIOLOGY