Long Term Outcomes of a Phase 1/2, Multicenter, Open-Label, Dose-Escalation Study to Evaluate the Safety, Tolerability, and Efficacy of BMN 110 in Patients with Mucopolysaccharidosis IVA (Morquio A Syndrome)

Title
Long Term Outcomes of a Phase 1/2, Multicenter, Open-Label, Dose-Escalation Study to Evaluate the Safety, Tolerability, and Efficacy of BMN 110 in Patients with Mucopolysaccharidosis IVA (Morquio A Syndrome)
Authors
Keywords
-
Journal
MOLECULAR GENETICS AND METABOLISM
Volume 105, Issue 2, Pages S35
Publisher
Elsevier BV
Online
2012-01-20
DOI
10.1016/j.ymgme.2011.11.076

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