A phase 1 trial of recombinant human acid Sphingomyelinase (rhASM) Enzyme replacement therapy in adults with Non-Neuronopathic ASM deficiency (ASMD Niemann-Pick B)

Title
A phase 1 trial of recombinant human acid Sphingomyelinase (rhASM) Enzyme replacement therapy in adults with Non-Neuronopathic ASM deficiency (ASMD Niemann-Pick B)
Authors
Keywords
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Journal
MOLECULAR GENETICS AND METABOLISM
Volume 102, Issue 2, Pages S28
Publisher
Elsevier BV
Online
2011-01-18
DOI
10.1016/j.ymgme.2010.11.095

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