Miglustat in adult and juvenile patients with Niemann–Pick disease type C: Long-term data from a clinical trial

Title
Miglustat in adult and juvenile patients with Niemann–Pick disease type C: Long-term data from a clinical trial
Authors
Keywords
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Journal
MOLECULAR GENETICS AND METABOLISM
Volume 99, Issue 4, Pages 351-357
Publisher
Elsevier BV
Online
2009-12-17
DOI
10.1016/j.ymgme.2009.12.006

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