Miglustat in patients with Niemann-Pick disease Type C (NP-C): A multicenter observational retrospective cohort study

Title
Miglustat in patients with Niemann-Pick disease Type C (NP-C): A multicenter observational retrospective cohort study
Authors
Keywords
-
Journal
MOLECULAR GENETICS AND METABOLISM
Volume 98, Issue 3, Pages 243-249
Publisher
Elsevier BV
Online
2009-07-12
DOI
10.1016/j.ymgme.2009.07.003

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