Sapropterin Is Safe and Effective in Patients less than 4-Years-Old with BH4-Responsive Phenylalanine Hydroxylase Deficiency

Title
Sapropterin Is Safe and Effective in Patients less than 4-Years-Old with BH4-Responsive Phenylalanine Hydroxylase Deficiency
Authors
Keywords
-
Journal
JOURNAL OF PEDIATRICS
Volume 165, Issue 6, Pages 1241-1244
Publisher
Elsevier BV
Online
2014-09-13
DOI
10.1016/j.jpeds.2014.08.003

Ask authors/readers for more resources

Find Funding. Review Successful Grants.

Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.

Explore

Add your recorded webinar

Do you already have a recorded webinar? Grow your audience and get more views by easily listing your recording on Peeref.

Upload Now