Recent progress in the understanding and treatment of transthyretin amyloidosis

Repurposing Diflunisal for Familial Amyloid Polyneuropathy

(2015) John L. Berk et al.   JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION

Synovial deposition of wild-type transthyretin-derived amyloid in knee joint osteoarthritis patients

(2013) Tetsuo Takanashi et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

High prevalence of ATTR amyloidosis in endomyocardial biopsy-proven cardiac amyloidosis patients

(2013) Michitaka Nakagawa et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Safety and Efficacy of RNAi Therapy for Transthyretin Amyloidosis

(2013) Teresa Coelho et al.   NEW ENGLAND JOURNAL OF MEDICINE

Amyloid fibril protein nomenclature: 2012 recommendations from the Nomenclature Committee of the International Society of Amyloidosis

(2012) Jean D. Sipe et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Clinical development of an antisense therapy for the treatment of transthyretin-associated polyneuropathy

(2012) Elizabeth J. Ackermann et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Tafamidis for transthyretin familial amyloid polyneuropathy: A randomized, controlled trial

(2012) T. Coelho et al.   NEUROLOGY

Long-term survival after liver transplantation in patients with familial amyloid polyneuropathy

(2012) T. Yamashita et al.   NEUROLOGY

Tafamidis, a potent and selective transthyretin kinetic stabilizer that inhibits the amyloid cascade

(2012) C. E. Bulawa et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Long-term data from the Familial Amyloidotic Polyneuropathy World Transplant Registry (FAPWTR)

(2011) H. E. Wilczek et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Wild-type transthyretin-derived amyloidosis in various ligaments and tendons

(2011) Takanao Sueyoshi et al.   HUMAN PATHOLOGY

High prevalence of wild-type transthyretin deposition in patients with idiopathic carpal tunnel syndrome: a common cause of carpal tunnel syndrome in the elderly

(2011) Yoshiki Sekijima et al.   HUMAN PATHOLOGY

Clinicopathological features of senile systemic amyloidosis: an ante- and post-mortem study

(2011) Mitsuharu Ueda et al.   MODERN PATHOLOGY

Suppression of choroid plexus transthyretin levels by antisense oligonucleotide treatment

(2010) Merrill D. Benson et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Biochemical effect of liver transplantation in two Swedish patients with familial amyloidotic polyneuropathy (FAP-met30)

(2010) Gösta Holmgren et al.   CLINICAL GENETICS

Heterogeneity of penetrance in familial amyloid polyneuropathy, ATTR Val30Met, in the Swedish population

(2008) Urban Hellman et al.   AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS

Quantification of the Thermodynamically Linked Quaternary and Tertiary Structural Stabilities of Transthyretin and Its Disease-Associated Variants: The Relationship between Stability and Amyloidosis†

(2008) Amy R. Hurshman Babbes et al.   BIOCHEMISTRY

Pathogenesis of and Therapeutic Strategies to Ameliorate the Transthyretin Amyloidoses

(2008) Yoshiki Sekijima et al.   CURRENT PHARMACEUTICAL DESIGN

Ten-year follow-up of peripheral nerve function in patients with familial amyloid polyneuropathy after liver transplantation

(2008) Y. Shimojima et al.   JOURNAL OF NEUROLOGY

Non-senile wild-type transthyretin systemic amyloidosis presenting as bilateral carpal tunnel syndrome

(2008)   JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM

Marked regression of abdominal fat amyloid in patients with familial amyloid polyneuropathy during long-term follow-up after liver transplantation

(2008) Ayako Tsuchiya et al.   LIVER TRANSPLANTATION