Intrathecal 2-hydroxypropyl-beta-cyclodextrin in a single patient with Niemann–Pick C1

Title
Intrathecal 2-hydroxypropyl-beta-cyclodextrin in a single patient with Niemann–Pick C1
Authors
Keywords
Niemann–Pick C, Cyclodextrin, Therapeutic, Ototoxicity
Journal
MOLECULAR GENETICS AND METABOLISM
Volume 116, Issue 1-2, Pages 75-79
Publisher
Elsevier BV
Online
2015-07-17
DOI
10.1016/j.ymgme.2015.07.001

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