Lysosomal storage disease: Gene therapy on both sides of the blood–brain barrier

Title
Lysosomal storage disease: Gene therapy on both sides of the blood–brain barrier
Authors
Keywords
Behavior, CNS, Neurologic, Mucopolysaccharidosis, Sleeping Beauty, transposon, Transcytosis
Journal
MOLECULAR GENETICS AND METABOLISM
Volume 114, Issue 2, Pages 83-93
Publisher
Elsevier BV
Online
2014-10-09
DOI
10.1016/j.ymgme.2014.09.011

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