Self-Assembly of a Multifunctional Lipid With Core-Shell Dendrimer DNA Nanoparticles Enhanced Efficient Gene Delivery at Low Charge Ratios into RPE Cells

Silencing β3 Integrin by Targeted ECO/siRNA Nanoparticles Inhibits EMT and Metastasis of Triple-Negative Breast Cancer

(2015) Jenny G. Parvani et al.   CANCER RESEARCH

Cationic Lipids as Transfecting Agents of DNA in Gene Therapy

(2014) Elena Junquera et al.   CURRENT TOPICS IN MEDICINAL CHEMISTRY

Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

(2014) Robert E MacLaren et al.   LANCET

Multifunctional Cationic Lipid-Based Nanoparticles Facilitate Endosomal Escape and Reduction-Triggered Cytosolic siRNA Release

(2014) Maneesh Gujrati et al.   MOLECULAR PHARMACEUTICS

Dendritic nanoglobules with polyhedral oligomeric silsesquioxane core and their biomedical applications

(2014) Zhuxian Zhou et al.   Nanomedicine

The Role of Surface Functionality in Determining Nanoparticle Cytotoxicity

(2013) Sung Tae Kim et al.   ACCOUNTS OF CHEMICAL RESEARCH

Synthesis and Evaluation of a Nanoglobular Dendrimer 5-Aminosalicylic Acid Conjugate with a Hydrolyzable Schiff Base Spacer for Treating Retinal Degeneration

(2013) Xueming Wu et al.   ACS Nano

Multiple Internalization Pathways of Polyelectrolyte Multilayer Capsules into Mammalian Cells

(2013) Lena Kastl et al.   ACS Nano

pH-Triggered Nanoparticle Mediated Delivery of siRNA to Liver Cells in Vitro and in Vivo

(2013) Soumia Kolli et al.   BIOCONJUGATE CHEMISTRY

A review of therapeutic prospects of non-viral gene therapy in the retinal pigment epithelium

(2013) Adarsha Koirala et al.   BIOMATERIALS

Successful Gene Therapy in Older Rpe65-Deficient Dogs Following Subretinal Injection of an Adeno-Associated Vector Expressing RPE65

(2013) Matthew J. Annear et al.   HUMAN GENE THERAPY

Design and evaluation of new pH-sensitive amphiphilic cationic lipids for siRNA delivery

(2013) Anthony S. Malamas et al.   JOURNAL OF CONTROLLED RELEASE

A Comprehensive Review of Retinal Gene Therapy

(2013) Shannon E Boye et al.   MOLECULAR THERAPY

Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement

(2013) A. V. Cideciyan et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Intracellular siRNA delivery with novel spermine based surfactants

(2012) RongZuo Xu et al.   CHINESE SCIENCE BULLETIN

Viral vectors for targeting the canine retina: a review

(2012) Simon M. Petersen-Jones   VETERINARY OPHTHALMOLOGY

Design, synthesis and evaluation of spermine-based pH-sensitive amphiphilic gene delivery systems: Multifunctional non-viral gene carriers

(2011) RongZuo Xu et al.   Science China-Chemistry

New Amphiphilic Carriers Forming pH-Sensitive Nanoparticles for Nucleic Acid Delivery

(2010) Rongzuo Xu et al.   LANGMUIR

Poly(oligo-D-arginine) With Internal Disulfide Linkages as a Cytoplasm-sensitive Carrier for siRNA Delivery

(2010) Young-Wook Won et al.   MOLECULAR THERAPY

Dendrimers in gene transfection

(2009) D. G. Shcharbin et al.   BIOCHEMISTRY-MOSCOW

Effect of innate glutathione levels on activity of redox-responsive gene delivery vectors

(2009) Devika S. Manickam et al.   JOURNAL OF CONTROLLED RELEASE

Toll-Like Receptor Prestimulation Increases Phagocytosis of Escherichia coli DH5  and Escherichia coli K1 Strains by Murine Microglial Cells

(2008) S. Ribes et al.   INFECTION AND IMMUNITY

Evaluation of the effect of vector architecture on DNA condensation and gene transfer efficiency

(2008) Brenda F. Canine et al.   JOURNAL OF CONTROLLED RELEASE

Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis

(2008) Albert M. Maguire et al.   NEW ENGLAND JOURNAL OF MEDICINE

Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

(2008) James W.B. Bainbridge et al.   NEW ENGLAND JOURNAL OF MEDICINE