In Vitro Correction of a Pseudoexon-Generating Deep Intronic Mutation in LGMD2A by Antisense Oligonucleotides and Modified Small Nuclear RNAs
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Title
In Vitro Correction of a Pseudoexon-Generating Deep Intronic Mutation in LGMD2A by Antisense Oligonucleotides and Modified Small Nuclear RNAs
Authors
Keywords
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Journal
HUMAN MUTATION
Volume 34, Issue 10, Pages 1387-1395
Publisher
Wiley
Online
2013-07-17
DOI
10.1002/humu.22379
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