Trans-splicing correction of tau isoform imbalance in a mouse model of tau mis-splicing

Tau alternative splicing in familial and sporadic tauopathies

(2012) Michael Niblock et al.   BIOCHEMICAL SOCIETY TRANSACTIONS

Spliceosome-Mediated Trans-Splicing: The Therapeutic Cut and Paste

(2012) Verena Wally et al.   JOURNAL OF INVESTIGATIVE DERMATOLOGY

Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis

(2012) Holly B. Kordasiewicz et al.   NEURON

Targeting a pre-mRNA structure with bipartite antisense molecules modulates tau alternative splicing

(2012) Eleanor Peacey et al.   NUCLEIC ACIDS RESEARCH

Antisense oligonucleotide therapeutics for inherited neurodegenerative diseases

(2012) Amber L. Southwell et al.   TRENDS IN MOLECULAR MEDICINE

Understanding the role of TDP-43 and FUS/TLS in ALS and beyond

(2011) Sandrine Da Cruz et al.   CURRENT OPINION IN NEUROBIOLOGY

Advances in tau-based drug discovery

(2011) Wendy Noble et al.   Expert Opinion on Drug Discovery

Trans-Splicing, More Than Meets the Eye: Multifaceted Therapeutics for Spinal Muscular Atrophy

(2011) Matthew E.R. Butchbach   HUMAN GENE THERAPY

The Many Faces of Tau

(2011) Meaghan Morris et al.   NEURON

Genetic therapies for RNA mis-splicing diseases

(2011) Suzan M. Hammond et al.   TRENDS IN GENETICS

Aberrant RNA processing events in neurological disorders

(2010) Karen Anthony et al.   BRAIN RESEARCH

Combination of SMN Trans-Splicing and a Neurotrophic Factor Increases the Life Span and Body Mass in a Severe Model of Spinal Muscular Atrophy

(2010) Monir Shababi et al.   HUMAN GENE THERAPY

K14 mRNA reprogramming for dominant epidermolysis bullosa simplex

(2010) Verena Wally et al.   HUMAN MOLECULAR GENETICS

Correction of tau mis-splicing caused by FTDP-17 MAPT mutations by spliceosome-mediated RNA trans-splicing

(2009) T. Rodriguez-Martin et al.   HUMAN MOLECULAR GENETICS

Tau isoform regulation is region- and cell-specific in mouse brain

(2008) Pamela McMillan et al.   JOURNAL OF COMPARATIVE NEUROLOGY

Development of a Single Vector System that Enhances Trans-Splicing of SMN2 Transcripts

(2008) Tristan H. Coady et al.   PLoS One

Interplay of  2* nicotinic receptors and dopamine pathways in the control of spontaneous locomotion

(2008) M. E. Avale et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA