Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

Dysferlin associates with the developing T-tubule system in rodent and human skeletal muscle

(2010) Lars Klinge et al.   MUSCLE & NERVE

Dysferlin Deficiency Enhances Monocyte Phagocytosis

(2008) Kanneboyina Nagaraju et al.   AMERICAN JOURNAL OF PATHOLOGY

Dysferlin Deficiency Shows Compensatory Induction of Rab27A/Slp2a That May Contribute to Inflammatory Onset

(2008) Akanchha Kesari et al.   AMERICAN JOURNAL OF PATHOLOGY

Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice

(2008) Mariacarmela Allocca et al.   JOURNAL OF CLINICAL INVESTIGATION

Engineering and Selection of Shuffled AAV Genomes: A New Strategy for Producing Targeted Biological Nanoparticles

(2008) Wuping Li et al.   MOLECULAR THERAPY

Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection

(2008) Carmela Zincarelli et al.   MOLECULAR THERAPY

Lack of toxicity of alpha-sarcoglycan overexpression supports clinical gene transfer trial in LGMD2D

(2008) L. R. Rodino-Klapac et al.   NEUROLOGY

A new phenotype of dysferlinopathy with congenital onset

(2008) C. Paradas et al.   NEUROMUSCULAR DISORDERS

Antibody-dependent enhancement of adeno-associated virus infection of human monocytic cell lines

(2008) Seiichiro Mori et al.   VIROLOGY