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Title
Combined Rod and Cone Transduction by Adeno-Associated Virus 2/8
Authors
Keywords
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Journal
HUMAN GENE THERAPY
Volume 24, Issue 12, Pages 982-992
Publisher
Mary Ann Liebert Inc
Online
2013-09-26
DOI
10.1089/hum.2013.154
References
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Related references
Note: Only part of the references are listed.- Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2
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- (2012) Samuel G. Jacobson et al. HUMAN MOLECULAR GENETICS
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- (2012) W. A. Beltran et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
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- Novel adeno-associated viral vectors for retinal gene therapy
- (2011) L H Vandenberghe et al. GENE THERAPY
- AAV-mediated photoreceptor transduction of the pig cone-enriched retina
- (2011) C Mussolino et al. GENE THERAPY
- Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency
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- MicroRNA-Restricted Transgene Expression in the Retina
- (2011) Marianthi Karali et al. PLoS One
- Dosage Thresholds for AAV2 and AAV8 Photoreceptor Gene Therapy in Monkey
- (2011) L. H. Vandenberghe et al. Science Translational Medicine
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- (2011) Mathias W. Seeliger et al. Nature Communications
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- Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial
- (2009) Albert M Maguire et al. LANCET
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- Vision 1 Year after Gene Therapy for Leber's Congenital Amaurosis
- (2009) Artur V. Cideciyan et al. NEW ENGLAND JOURNAL OF MEDICINE
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- (2008) Corinna Lebherz et al. JOURNAL OF GENE MEDICINE
- Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
- (2008) Albert M. Maguire et al. NEW ENGLAND JOURNAL OF MEDICINE
- Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis
- (2008) James W.B. Bainbridge et al. NEW ENGLAND JOURNAL OF MEDICINE
- Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics
- (2008) A. V. Cideciyan et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Leber congenital amaurosis: Genes, proteins and disease mechanisms
- (2008) Anneke I. den Hollander et al. PROGRESS IN RETINAL AND EYE RESEARCH
- Versatility of AAV vectors for retinal gene transfer
- (2007) Enrico M. Surace et al. VISION RESEARCH
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