A validated cellular biobank for β-thalassemia

Prospective isolation of human erythroid lineage-committed progenitors

(2015) Yasuo Mori et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Heritable CRISPR/Cas9-Mediated Genome Editing in the Yellow Fever Mosquito, Aedes aegypti

(2015) Shengzhang Dong et al.   PLoS One

Isolation and transcriptome analyses of human erythroid progenitors: BFU-E and CFU-E

(2014) J. Li et al.   BLOOD

SAPTA: a new design tool for improving TALE nuclease activity

(2014) Yanni Lin et al.   NUCLEIC ACIDS RESEARCH

Transcription Activator-like Effector Nuclease (TALEN)-mediated Gene Correction in Integration-free β-Thalassemia Induced Pluripotent Stem Cells

(2013) Ning Ma et al.   JOURNAL OF BIOLOGICAL CHEMISTRY

ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

(2013) Thomas Gaj et al.   TRENDS IN BIOTECHNOLOGY

A combined approach for β-thalassemia based on gene therapy-mediated adult hemoglobin (HbA) production and fetal hemoglobin (HbF) induction

(2012) Cristina Zuccato et al.   ANNALS OF HEMATOLOGY

Network-based drug discovery by integrating systems biology and computational technologies

(2012) E. L. Leung et al.   BRIEFINGS IN BIOINFORMATICS

TALE nucleases: tailored genome engineering made easy

(2012) Claudio Mussolino et al.   CURRENT OPINION IN BIOTECHNOLOGY

Therapeutic Hemoglobin Levels after Gene Transfer in β-Thalassemia Mice and in Hematopoietic Cells of β-Thalassemia and Sickle Cells Disease Patients

(2012) Laura Breda et al.   PLoS One

Site-specific integration and tailoring of cassette design for sustainable gene transfer

(2011) Angelo Lombardo et al.   NATURE METHODS

Using electronic health records to drive discovery in disease genomics

(2011) Isaac S. Kohane   NATURE REVIEWS GENETICS

A novel TALE nuclease scaffold enables high genome editing activity in combination with low toxicity

(2011) Claudio Mussolino et al.   NUCLEIC ACIDS RESEARCH

A preclinical approach for gene therapy of β-thalassemia

(2010) Laura Breda et al.   Annals of the New York Academy of Sciences

Biobanking: the foundation of personalized medicine

(2010) Robert E Hewitt   CURRENT OPINION IN ONCOLOGY

Collaboration and competition between DNA double-strand break repair pathways

(2010) Elizabeth M. Kass et al.   FEBS LETTERS

Resolving the distinct stages in erythroid differentiation based on dynamic changes in membrane protein expression during erythropoiesis

(2009) K. Chen et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Stem Cell Engineering for the Treatment of Severe Hemoglobinopathies

(2008) Michel Sadelain et al.   CURRENT MOLECULAR MEDICINE

Biobanking for better healthcare

(2008) Peter H.J. Riegman et al.   Molecular Oncology

Biobanken und Biomolekulare Ressourcen Forschungsinfrastruktur (BBMRI)

(2008) C. Viertler et al.   PATHOLOGE