Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome
出版年份 2021 全文链接
标题
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome
作者
关键词
-
出版物
EMBO Molecular Medicine
Volume -, Issue -, Pages -
出版商
EMBO
发表日期
2021-01-22
DOI
10.15252/emmm.202013545
参考文献
相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。- CRISPR-engineered T cells in patients with refractory cancer
- (2020) Edward A. Stadtmauer et al. SCIENCE
- Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking
- (2020) Samuele Ferrari et al. NATURE BIOTECHNOLOGY
- Hematopoietic stem cell transplantation for CD40 ligand deficiency: results from an EBMT/ESID-IEWP-SCETIDE-PIDTC Study
- (2019) Francesca Ferrua et al. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY
- Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
- (2019) Christopher E. Nelson et al. NATURE MEDICINE
- Combined liver and hematopoietic stem cell transplantation in patients with X-linked hyper-IgM syndrome
- (2019) Giorgia Bucciol et al. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY
- The Contribution of Host Cells to Pneumocystis Immunity: An Update
- (2019) Patricia Otieno-Odhiambo et al. Pathogens
- Next generation chimeric antigen receptor T cells: safety strategies to overcome toxicity
- (2019) Shengnan Yu et al. Molecular Cancer
- High levels of AAV vector integration into CRISPR-induced DNA breaks
- (2019) Killian S. Hanlon et al. Nature Communications
- UDiTaS™, a genome editing detection method for indels and genome rearrangements
- (2018) Georgia Giannoukos et al. BMC GENOMICS
- Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome
- (2018) Caroline Y. Kuo et al. Cell Reports
- Embracing microbial exposure in mouse research
- (2018) Mathew A. Huggins et al. JOURNAL OF LEUKOCYTE BIOLOGY
- How introns enhance gene expression
- (2017) Orit Shaul INTERNATIONAL JOURNAL OF BIOCHEMISTRY & CELL BIOLOGY
- Long-term outcomes of 176 patients with X-linked hyper-IgM syndrome treated with or without hematopoietic cell transplantation
- (2017) M. Teresa de la Morena et al. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY
- A novel hemolytic complement-sufficient NSG mouse model supports studies of complement-mediated antitumor activity in vivo
- (2017) Mohit K. Verma et al. JOURNAL OF IMMUNOLOGICAL METHODS
- T memory stem cells in health and disease
- (2017) Luca Gattinoni et al. NATURE MEDICINE
- CRISPR-Cas9 gene repair of hematopoietic stem cells from patients with X-linked chronic granulomatous disease
- (2017) Suk See De Ravin et al. Science Translational Medicine
- Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1
- (2017) Giulia Schiroli et al. Science Translational Medicine
- Targeted gene editing restores regulated CD40L function in X-linked hyper-IgM syndrome
- (2016) Nicholas Hubbard et al. BLOOD
- Targeted antibody-mediated depletion of murine CD19 CAR T cells permanently reverses B cell aplasia
- (2016) Paulina J. Paszkiewicz et al. JOURNAL OF CLINICAL INVESTIGATION
- CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells
- (2016) Daniel P. Dever et al. NATURE
- Non-genotoxic conditioning for hematopoietic stem cell transplantation using a hematopoietic-cell-specific internalizing immunotoxin
- (2016) Rahul Palchaudhuri et al. NATURE BIOTECHNOLOGY
- Digenome-seq: genome-wide profiling of CRISPR-Cas9 off-target effects in human cells
- (2015) Daesik Kim et al. NATURE METHODS
- Highly efficient homology-driven genome editing in human T cells by combining zinc-finger nuclease mRNA and AAV6 donor delivery
- (2015) Jianbin Wang et al. NUCLEIC ACIDS RESEARCH
- Tracking genetically engineered lymphocytes long-term reveals the dynamics of T cell immunological memory
- (2015) Giacomo Oliveira et al. Science Translational Medicine
- Targeted genome editing in human repopulating haematopoietic stem cells
- (2014) Pietro Genovese et al. NATURE
- Promoterless gene targeting without nucleases ameliorates haemophilia B in mice
- (2014) A. Barzel et al. NATURE
- GUIDE-seq enables genome-wide profiling of off-target cleavage by CRISPR-Cas nucleases
- (2014) Shengdar Q Tsai et al. NATURE BIOTECHNOLOGY
- Gene Editing of CCR5 in Autologous CD4 T Cells of Persons Infected with HIV
- (2014) Pablo Tebas et al. NEW ENGLAND JOURNAL OF MEDICINE
- Quantifying the Effect of Ribosomal Density on mRNA Stability
- (2014) Shlomit Edri et al. PLoS One
- CD40L expression permits CD8+ T cells to execute immunologic helper functions
- (2013) M. Frentsch et al. BLOOD
- The Hyper IgM Syndromes
- (2013) Nashmia Qamar et al. CLINICAL REVIEWS IN ALLERGY & IMMUNOLOGY
- IL-7 and IL-15 instruct the generation of human memory stem T cells from naive precursors
- (2012) N. Cieri et al. BLOOD
- Discordant antibody and cellular responses to Pneumocystis major surface glycoprotein variants in mice
- (2012) Lisa R Bishop et al. BMC IMMUNOLOGY
- Adoptive Transfer of Epstein-Barr Virus (EBV) Nuclear Antigen 1–Specific T Cells As Treatment for EBV Reactivation and Lymphoproliferative Disorders After Allogeneic Stem-Cell Transplantation
- (2012) Vanya Icheva et al. JOURNAL OF CLINICAL ONCOLOGY
- Fast gapped-read alignment with Bowtie 2
- (2012) Ben Langmead et al. NATURE METHODS
- Immune reconstitution inflammatory syndrome: the trouble with immunity when you had none
- (2012) Daniel L. Barber et al. NATURE REVIEWS MICROBIOLOGY
- Primer3—new capabilities and interfaces
- (2012) Andreas Untergasser et al. NUCLEIC ACIDS RESEARCH
- A transgene-encoded cell surface polypeptide for selection, in vivo tracking, and ablation of engineered cells
- (2011) X. Wang et al. BLOOD
- Natural killer (NK):dendritic cell (DC) cross talk induced by therapeutic monoclonal antibody triggers tumor antigen-specific T cell immunity
- (2011) Steve C. Lee et al. IMMUNOLOGIC RESEARCH
- In vivo genome editing restores haemostasis in a mouse model of haemophilia
- (2011) Hojun Li et al. NATURE
- A human memory T cell subset with stem cell–like properties
- (2011) Luca Gattinoni et al. NATURE MEDICINE
- Site-specific integration and tailoring of cassette design for sustainable gene transfer
- (2011) Angelo Lombardo et al. NATURE METHODS
- A tissue-specific, activation-inducible, lentiviral vector regulated by human CD40L proximal promoter sequences
- (2010) Z Romero et al. GENE THERAPY
- The safety and side effects of monoclonal antibodies
- (2010) Trevor T. Hansel et al. NATURE REVIEWS DRUG DISCOVERY
- The Sequence Alignment/Map format and SAMtools
- (2009) H. Li et al. BIOINFORMATICS
- Hematopoietic stem cell transplantation for pediatric patients with primary immunodeficiency diseases at All Children’s Hospital/University of South Florida
- (2009) A. Petrovic et al. IMMUNOLOGIC RESEARCH
Publish scientific posters with Peeref
Peeref publishes scientific posters from all research disciplines. Our Diamond Open Access policy means free access to content and no publication fees for authors.
Learn MoreFind the ideal target journal for your manuscript
Explore over 38,000 international journals covering a vast array of academic fields.
Search