标题
Targeted genome editing in human repopulating haematopoietic stem cells
作者
关键词
-
出版物
NATURE
Volume 510, Issue 7504, Pages 235-240
出版商
Springer Nature
发表日期
2014-05-29
DOI
10.1038/nature13420
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- CRISPR-Cas systems for editing, regulating and targeting genomes
- (2014) Jeffry D Sander et al. NATURE BIOTECHNOLOGY
- Gene Editing of CCR5 in Autologous CD4 T Cells of Persons Infected with HIV
- (2014) Pablo Tebas et al. NEW ENGLAND JOURNAL OF MEDICINE
- Gene Therapy for Wiskott-Aldrich Syndrome--Long-Term Efficacy and Genotoxicity
- (2014) C. J. Braun et al. Science Translational Medicine
- Genetic Engineering of Hematopoiesis for Targeted IFN- Delivery Inhibits Breast Cancer Progression
- (2014) G. Escobar et al. Science Translational Medicine
- Long-term human immune system reconstitution in non-obese diabetic (NOD)-Rag (-)-γ chain (-) (NRG) mice is similar but not identical to the original stem cell donor
- (2013) D. T. Harris et al. CLINICAL AND EXPERIMENTAL IMMUNOLOGY
- Gene therapy for PIDs: Progress, pitfalls and prospects
- (2013) Sayandip Mukherjee et al. GENE
- Mechanisms of Retroviral Integration and Mutagenesis
- (2013) Alessia Cavazza et al. HUMAN GENE THERAPY
- Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
- (2013) A. Aiuti et al. SCIENCE
- Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
- (2013) A. Biffi et al. SCIENCE
- IL-7 and IL-15 instruct the generation of human memory stem T cells from naive precursors
- (2012) N. Cieri et al. BLOOD
- Hematopoiesis: A Human Perspective
- (2012) Sergei Doulatov et al. Cell Stem Cell
- Editing T cell specificity towards leukemia by zinc finger nucleases and lentiviral gene transfer
- (2012) Elena Provasi et al. NATURE MEDICINE
- TALENs: a widely applicable technology for targeted genome editing
- (2012) J. Keith Joung et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- BamTools: a C++ API and toolkit for analyzing and managing BAM files
- (2011) D. W. Barnett et al. BIOINFORMATICS
- Oxidase-deficient neutrophils from X-linked chronic granulomatous disease iPS cells: functional correction by zinc finger nuclease-mediated safe harbor targeting
- (2011) J. Zou et al. BLOOD
- Prostaglandin E2 Enhances Human Cord Blood Stem Cell Xenotransplants and Shows Long-Term Safety in Preclinical Nonhuman Primate Transplant Models
- (2011) Wolfram Goessling et al. Cell Stem Cell
- Hepatocyte-targeted expression by integrase-defective lentiviral vectors induces antigen-specific tolerance in mice with low genotoxic risk
- (2011) Janka Mátrai et al. HEPATOLOGY
- In vivo genome editing restores haemostasis in a mouse model of haemophilia
- (2011) Hojun Li et al. NATURE
- An unbiased genome-wide analysis of zinc-finger nuclease specificity
- (2011) Richard Gabriel et al. NATURE BIOTECHNOLOGY
- A human memory T cell subset with stem cell–like properties
- (2011) Luca Gattinoni et al. NATURE MEDICINE
- Site-specific integration and tailoring of cassette design for sustainable gene transfer
- (2011) Angelo Lombardo et al. NATURE METHODS
- Ex vivo gene transfer and correction for cell-based therapies
- (2011) Luigi Naldini NATURE REVIEWS GENETICS
- A novel TALE nuclease scaffold enables high genome editing activity in combination with low toxicity
- (2011) Claudio Mussolino et al. NUCLEIC ACIDS RESEARCH
- A Distinctive DNA Damage Response in Human Hematopoietic Stem Cells Reveals an Apoptosis-Independent Role for p53 in Self-Renewal
- (2010) Michael Milyavsky et al. Cell Stem Cell
- Hematopoietic Stem Cell Quiescence Promotes Error-Prone DNA Repair and Mutagenesis
- (2010) Mary Mohrin et al. Cell Stem Cell
- The DNA Damage Response: Making It Safe to Play with Knives
- (2010) Alberto Ciccia et al. MOLECULAR CELL
- Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
- (2010) Marina Cavazzana-Calvo et al. NATURE
- Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo
- (2010) Nathalia Holt et al. NATURE BIOTECHNOLOGY
- Genome editing with engineered zinc finger nucleases
- (2010) Fyodor D. Urnov et al. NATURE REVIEWS GENETICS
- Aryl Hydrocarbon Receptor Antagonists Promote the Expansion of Human Hematopoietic Stem Cells
- (2010) Anthony E. Boitano et al. SCIENCE
- Identification of Hematopoietic Stem Cell-Specific miRNAs Enables Gene Therapy of Globoid Cell Leukodystrophy
- (2010) B. Gentner et al. Science Translational Medicine
- The Sequence Alignment/Map format and SAMtools
- (2009) H. Li et al. BIOINFORMATICS
- Fast and accurate short read alignment with Burrows-Wheeler transform
- (2009) H. Li et al. BIOINFORMATICS
- Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases
- (2009) Dirk Hockemeyer et al. NATURE BIOTECHNOLOGY
- Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
- (2009) N. Cartier et al. SCIENCE
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