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Mechanisms of Retroviral Integration and Mutagenesis

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A Mini-intronic Plasmid (MIP): A Novel Robust Transgene Expression Vector In Vivo and In Vitro

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High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

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Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

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In Vivo-Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous

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AAV-Mediated Gene Targeting Is Significantly Enhanced by Transient Inhibition of Nonhomologous End Joining or the Proteasome In Vivo

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Single Amino Acid Modification of Adeno-Associated Virus Capsid Changes Transduction and Humoral Immune Profiles

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Ribosomal DNA Integrating rAAV-rDNA Vectors Allow for Stable Transgene Expression

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Antibody-based protection against HIV infection by vectored immunoprophylaxis

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In vivo genome editing restores haemostasis in a mouse model of haemophilia

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Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

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High Cleavage Efficiency of a 2A Peptide Derived from Porcine Teschovirus-1 in Human Cell Lines, Zebrafish and Mice

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Gene therapy with human and mouse T-cell receptors mediates cancer regression and targets normal tissues expressing cognate antigen

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Adeno-associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo

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Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

(2008) Salima Hacein-Bey-Abina et al.   JOURNAL OF CLINICAL INVESTIGATION

In Vitro and In Vivo Gene Therapy Vector Evolution via Multispecies Interbreeding and Retargeting of Adeno-Associated Viruses

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A reproducible and well-tolerated method for 2/3 partial hepatectomy in mice

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