Prolonged cultured human hepatocytes as an in vitro experimental system for the evaluation of potency and duration of activity of RNA therapeutics: Demonstration of prolonged duration of gene silencing effects of a GalNAc-conjugated human hypoxanthine phosphoribosyl transferase (HPRT1) siRNA
出版年份 2020 全文链接
标题
Prolonged cultured human hepatocytes as an in vitro experimental system for the evaluation of potency and duration of activity of RNA therapeutics: Demonstration of prolonged duration of gene silencing effects of a GalNAc-conjugated human hypoxanthine phosphoribosyl transferase (HPRT1) siRNA
作者
关键词
RNA therapeutics, Gal-Nac conjugated siRNA, Prolonged cultured human hepatocytes, 999Elite human hepatocytes, Hypoxanthine phosphoribosyl transferase 1
出版物
BIOCHEMICAL PHARMACOLOGY
Volume -, Issue -, Pages 114374
出版商
Elsevier BV
发表日期
2020-12-31
DOI
10.1016/j.bcp.2020.114374
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