Non-viral and viral delivery systems for CRISPR-Cas9 technology in the biomedical field
出版年份 2017 全文链接
标题
Non-viral and viral delivery systems for CRISPR-Cas9 technology in the biomedical field
作者
关键词
genome editing, CRISPR, Cas9, viral vector, non-viral vector, gene therapy
出版物
Science China-Life Sciences
Volume 60, Issue 5, Pages 458-467
出版商
Springer Nature
发表日期
2017-05-19
DOI
10.1007/s11427-017-9033-0
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Cpf1 nucleases demonstrate robust activity to induce DNA modification by exploiting homology directed repair pathways in mammalian cells
- (2016) Eszter Tóth et al. Biology Direct
- CRISPR (Clustered Regularly Interspaced Palindromic Repeat)/Cas9 System
- (2016) Nikhil V. Munshi CIRCULATION
- Highly multiplexed CRISPR-Cas9-nuclease and Cas9-nickase vectors for inactivation of hepatitis B virus
- (2016) Tetsushi Sakuma et al. GENES TO CELLS
- In Vivo Delivery Systems for Therapeutic Genome Editing
- (2016) Luyao Wang et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Delivery methods for site-specific nucleases: Achieving the full potential of therapeutic gene editing
- (2016) Jia Liu et al. JOURNAL OF CONTROLLED RELEASE
- CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx Mice
- (2016) Li Xu et al. MOLECULAR THERAPY
- Chinese scientists to pioneer first human CRISPR trial
- (2016) David Cyranoski NATURE
- Frizzled proteins are colonic epithelial receptors for C. difficile toxin B
- (2016) Liang Tao et al. NATURE
- High-fidelity CRISPR–Cas9 nucleases with no detectable genome-wide off-target effects
- (2016) Benjamin P. Kleinstiver et al. NATURE
- A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
- (2016) Yang Yang et al. NATURE BIOTECHNOLOGY
- Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo
- (2016) Hao Yin et al. NATURE BIOTECHNOLOGY
- Efficient genome engineering approaches for the short-lived African turquoise killifish
- (2016) Itamar Harel et al. Nature Protocols
- Epigenomic engineering for Down syndrome
- (2016) A.F. Mentis NEUROSCIENCE AND BIOBEHAVIORAL REVIEWS
- CRISPR-Cas: biology, mechanisms and relevance
- (2016) Frank Hille et al. PHILOSOPHICAL TRANSACTIONS OF THE ROYAL SOCIETY B-BIOLOGICAL SCIENCES
- DNA-guided genome editing tool
- (2016) Dandan Zhang et al. Science China-Life Sciences
- From the first human gene-editing to the birth of three-parent baby
- (2016) Xiaoxue Zhang et al. Science China-Life Sciences
- Advances in therapeutic CRISPR/Cas9 genome editing
- (2016) Nataša Savić et al. Translational Research
- Editing of mouse and human immunoglobulin genes by CRISPR-Cas9 system
- (2016) Taek-Chin Cheong et al. Nature Communications
- A Retroviral CRISPR-Cas9 System for Cellular Autism-Associated Phenotype Discovery in Developing Neurons
- (2016) Michael R. Williams et al. Scientific Reports
- Super-Enhancers at the Nanog Locus Differentially Regulate Neighboring Pluripotency-Associated Genes
- (2016) Steven Blinka et al. Cell Reports
- Designing, Packaging, and Delivery of High Titer CRISPR Retro and Lentiviruses via Stereotaxic Injection
- (2016) Catherine J. Fricano-Kugler et al. Jove-Journal of Visualized Experiments
- CRISPR-Cas9 directed knock-out of a constitutively expressed gene using lance array nanoinjection
- (2016) John W. Sessions et al. SpringerPlus
- Somatic cell reprogramming-free generation of genetically modified pigs
- (2016) F. Tanihara et al. Science Advances
- Generation of VDR Knock-Out Mice via Zygote Injection of CRISPR/Cas9 System
- (2016) Tao Zhang et al. PLoS One
- Ovarian cancer treatment with a tumor-targeting and gene expression-controllable lipoplex
- (2016) Zhi-Yao He et al. Scientific Reports
- CRISPR-Cas9 mediated efficient PD-1 disruption on human primary T cells from cancer patients
- (2016) Shu Su et al. Scientific Reports
- Optimization of CRISPR/Cas9 genome editing to modify abiotic stress responses in plants
- (2016) Yuriko Osakabe et al. Scientific Reports
- A novel technique based on in vitro oocyte injection to improve CRISPR/Cas9 gene editing in zebrafish
- (2016) Shao-Lin Xie et al. Scientific Reports
- CRISPR/Cas9-Mediated Genome Editing of Epigenetic Factors for Cancer Therapy
- (2015) Shaohua Yao et al. HUMAN GENE THERAPY
- Adenovirus-Mediated Somatic Genome Editing ofPtenby CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune Responses
- (2015) Dan Wang et al. HUMAN GENE THERAPY
- Efficiently Editing the Vaccinia Virus Genome by Using the CRISPR-Cas9 System
- (2015) Ming Yuan et al. JOURNAL OF VIROLOGY
- In vivo genome editing using Staphylococcus aureus Cas9
- (2015) F. Ann Ran et al. NATURE
- Increasing the efficiency of precise genome editing with CRISPR-Cas9 by inhibition of nonhomologous end joining
- (2015) Takeshi Maruyama et al. NATURE BIOTECHNOLOGY
- Small molecule–triggered Cas9 protein with improved genome-editing specificity
- (2015) Kevin M Davis et al. Nature Chemical Biology
- Therapeutic genome editing: prospects and challenges
- (2015) David Benjamin Turitz Cox et al. NATURE MEDICINE
- Development of an intein-mediated split–Cas9 system for gene therapy
- (2015) Dong-Jiunn Jeffery Truong et al. NUCLEIC ACIDS RESEARCH
- Generation of knock-in primary human T cells using Cas9 ribonucleoproteins
- (2015) Kathrin Schumann et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Rationally engineered Cas9 nucleases with improved specificity
- (2015) I. M. Slaymaker et al. SCIENCE
- Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy
- (2015) C. Long et al. SCIENCE
- In vivo gene editing in dystrophic mouse muscle and muscle stem cells
- (2015) M. Tabebordbar et al. SCIENCE
- In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
- (2015) C. E. Nelson et al. SCIENCE
- Translational Medicine Center of West China Hospital
- (2015) Hongxin Deng et al. Science China-Life Sciences
- Suppression of hepatitis B virus DNA accumulation in chronically infected cells using a bacterial CRISPR/Cas RNA-guided DNA endonuclease
- (2015) Edward M. Kennedy et al. VIROLOGY
- An Inducible Lentiviral Guide RNA Platform Enables the Identification of Tumor-Essential Genes and Tumor-Promoting Mutations In Vivo
- (2015) Brandon J. Aubrey et al. Cell Reports
- A marker-free system for highly efficient construction of vaccinia virus vectors using CRISPR Cas9
- (2015) Ming Yuan et al. Molecular Therapy-Methods & Clinical Development
- Crystal Structure of Cas9 in Complex with Guide RNA and Target DNA
- (2014) Hiroshi Nishimasu et al. CELL
- Generation of Gene-Modified Cynomolgus Monkey via Cas9/RNA-Mediated Gene Targeting in One-Cell Embryos
- (2014) Yuyu Niu et al. CELL
- Efficient Ablation of Genes in Human Hematopoietic Stem and Effector Cells using CRISPR/Cas9
- (2014) Pankaj K. Mandal et al. Cell Stem Cell
- Gene disruption by cell-penetrating peptide-mediated delivery of Cas9 protein and guide RNA
- (2014) S. Ramakrishna et al. GENOME RESEARCH
- Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins
- (2014) S. Kim et al. GENOME RESEARCH
- Targeting Cdk11 in osteosarcoma cells using the CRISPR-cas9 system
- (2014) Yong Feng et al. JOURNAL OF ORTHOPAEDIC RESEARCH
- Inactivation of the Human Papillomavirus E6 or E7 Gene in Cervical Carcinoma Cells by Using a Bacterial CRISPR/Cas RNA-Guided Endonuclease
- (2014) E. M. Kennedy et al. JOURNAL OF VIROLOGY
- Engineering large viral DNA genomes using the CRISPR-Cas9 system
- (2014) Tadahiro Suenaga et al. MICROBIOLOGY AND IMMUNOLOGY
- CRISPR-mediated direct mutation of cancer genes in the mouse liver
- (2014) Wen Xue et al. NATURE
- In vivo interrogation of gene function in the mammalian brain using CRISPR-Cas9
- (2014) Lukasz Swiech et al. NATURE BIOTECHNOLOGY
- Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo
- (2014) John A Zuris et al. NATURE BIOTECHNOLOGY
- Improving CRISPR-Cas nuclease specificity using truncated guide RNAs
- (2014) Yanfang Fu et al. NATURE BIOTECHNOLOGY
- Dimeric CRISPR RNA-guided FokI nucleases for highly specific genome editing
- (2014) Shengdar Q Tsai et al. NATURE BIOTECHNOLOGY
- Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype
- (2014) Hao Yin et al. NATURE BIOTECHNOLOGY
- CRISPR/Cas9 systems have off-target activity with insertions or deletions between target DNA and guide RNA sequences
- (2014) Y. Lin et al. NUCLEIC ACIDS RESEARCH
- Synthesizing AND gate genetic circuits based on CRISPR-Cas9 for identification of bladder cancer cells
- (2014) Yuchen Liu et al. Nature Communications
- Adenoviral vector delivery of RNA-guided CRISPR/Cas9 nuclease complexes induces targeted mutagenesis in a diverse array of human cells
- (2014) Ignazio Maggio et al. Scientific Reports
- The CRISPR/Cas9 System Facilitates Clearance of the Intrahepatic HBV Templates In Vivo
- (2014) Su-Ru Lin et al. Molecular Therapy-Nucleic Acids
- Analysis of off-target effects of CRISPR/Cas-derived RNA-guided endonucleases and nickases
- (2013) S. W. Cho et al. GENOME RESEARCH
- RNA-guided gene activation by CRISPR-Cas9–based transcription factors
- (2013) Pablo Perez-Pinera et al. NATURE METHODS
- Efficient multiplex biallelic zebrafish genome editing using a CRISPR nuclease system
- (2013) Li-En Jao et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Genome-Scale CRISPR-Cas9 Knockout Screening in Human Cells
- (2013) Ophir Shalem et al. SCIENCE
- Multiplex Genome Engineering Using CRISPR/Cas Systems
- (2013) L. Cong et al. SCIENCE
- ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering
- (2013) Thomas Gaj et al. TRENDS IN BIOTECHNOLOGY
- TALENs: a widely applicable technology for targeted genome editing
- (2012) J. Keith Joung et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- Safety, Activity, and Immune Correlates of Anti–PD-1 Antibody in Cancer
- (2012) Suzanne L. Topalian et al. NEW ENGLAND JOURNAL OF MEDICINE
- Nonviral Direct Conversion of Primary Mouse Embryonic Fibroblasts to Neuronal Cells
- (2012) Andrew F Adler et al. Molecular Therapy-Nucleic Acids
- The CRISPR/Cas bacterial immune system cleaves bacteriophage and plasmid DNA
- (2010) Josiane E. Garneau et al. NATURE
- Genome editing with engineered zinc finger nucleases
- (2010) Fyodor D. Urnov et al. NATURE REVIEWS GENETICS
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