Intravenous 2-hydroxypropyl-β-cyclodextrin (Trappsol® Cyclo™) demonstrates biological activity and impacts cholesterol metabolism in the central nervous system and peripheral tissues in adult subjects with Niemann-Pick Disease Type C1: Results of a phase 1 trial
出版年份 2022 全文链接
标题
Intravenous 2-hydroxypropyl-β-cyclodextrin (Trappsol® Cyclo™) demonstrates biological activity and impacts cholesterol metabolism in the central nervous system and peripheral tissues in adult subjects with Niemann-Pick Disease Type C1: Results of a phase 1 trial
作者
关键词
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出版物
MOLECULAR GENETICS AND METABOLISM
Volume 137, Issue 4, Pages 309-319
出版商
Elsevier BV
发表日期
2022-10-18
DOI
10.1016/j.ymgme.2022.10.004
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