Multiplex CRISPR/Cas9 genome editing in hematopoietic stem cells for fetal hemoglobin reinduction generates chromosomal translocations
出版年份 2021 全文链接
标题
Multiplex CRISPR/Cas9 genome editing in hematopoietic stem cells for fetal hemoglobin reinduction generates chromosomal translocations
作者
关键词
BCL11A, CRISPR/Cas9, fetal hemoglobin, genome editing, HBG, multiplex editing, sickle cell disease, thalassemia, translocations
出版物
Molecular Therapy-Methods & Clinical Development
Volume 23, Issue -, Pages 507-523
出版商
Elsevier BV
发表日期
2021-10-29
DOI
10.1016/j.omtm.2021.10.008
参考文献
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