Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
出版年份 2021 全文链接
标题
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
作者
关键词
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出版物
Science Translational Medicine
Volume 13, Issue 598, Pages eabf2444
出版商
American Association for the Advancement of Science (AAAS)
发表日期
2021-06-17
DOI
10.1126/scitranslmed.abf2444
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