Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment
出版年份 2021 全文链接
标题
Efficacy and safety of arimoclomol in
Niemann‐Pick
disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment
作者
关键词
-
出版物
JOURNAL OF INHERITED METABOLIC DISEASE
Volume -, Issue -, Pages -
出版商
Wiley
发表日期
2021-08-22
DOI
10.1002/jimd.12428
参考文献
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