FDA orphan drug designations for lysosomal storage disorders – a cross-sectional analysis
出版年份 2020 全文链接
标题
FDA orphan drug designations for lysosomal storage disorders – a cross-sectional analysis
作者
关键词
Lysosomes, Drug therapy, Drug research and development, Gaucher's disease, Gene therapy, Fabry disease, Small molecules, Enzyme replacement therapy
出版物
PLoS One
Volume 15, Issue 4, Pages e0230898
出版商
Public Library of Science (PLoS)
发表日期
2020-04-09
DOI
10.1371/journal.pone.0230898
参考文献
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