标题
CRISPR genome engineering and viral gene delivery: A case of mutual attraction
作者
关键词
-
出版物
Biotechnology Journal
Volume 10, Issue 2, Pages 258-272
出版商
Wiley
发表日期
2015-02-06
DOI
10.1002/biot.201400529
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Genome Engineering with Targetable Nucleases
- (2014) Dana Carroll Annual Review of Biochemistry
- CRISPR/Cas9-mediated genome engineering: An adeno-associated viral (AAV) vector toolbox
- (2014) Elena Senís et al. Biotechnology Journal
- CRISPR-Cas9 Knockin Mice for Genome Editing and Cancer Modeling
- (2014) Randall J. Platt et al. CELL
- Genome-Scale CRISPR-Mediated Control of Gene Repression and Activation
- (2014) Luke A. Gilbert et al. CELL
- Development and Applications of CRISPR-Cas9 for Genome Engineering
- (2014) Patrick D. Hsu et al. CELL
- Permanent Alteration of PCSK9 With In Vivo CRISPR-Cas9 Genome Editing
- (2014) Qiurong Ding et al. CIRCULATION RESEARCH
- Efficient gene editing in adult mouse livers via adenoviral delivery of CRISPR/Cas9
- (2014) Ranran Cheng et al. FEBS LETTERS
- Current status of haemophilia gene therapy
- (2014) K. H. High et al. HAEMOPHILIA
- Multiplexed and Programmable Regulation of Gene Networks with an Integrated RNA and CRISPR/Cas Toolkit in Human Cells
- (2014) Lior Nissim et al. MOLECULAR CELL
- Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo
- (2014) Daniela Cesana et al. MOLECULAR THERAPY
- Dual-regulated Lentiviral Vector for Gene Therapy of X-linked Chronic Granulomatosis
- (2014) Maria Chiriaco et al. MOLECULAR THERAPY
- High-throughput screening of a CRISPR/Cas9 library for functional genomics in human cells
- (2014) Yuexin Zhou et al. NATURE
- In vivo engineering of oncogenic chromosomal rearrangements with the CRISPR/Cas9 system
- (2014) Danilo Maddalo et al. NATURE
- In vivo interrogation of gene function in the mammalian brain using CRISPR-Cas9
- (2014) Lukasz Swiech et al. NATURE BIOTECHNOLOGY
- Improving CRISPR-Cas nuclease specificity using truncated guide RNAs
- (2014) Yanfang Fu et al. NATURE BIOTECHNOLOGY
- CRISPR-Cas systems for editing, regulating and targeting genomes
- (2014) Jeffry D Sander et al. NATURE BIOTECHNOLOGY
- Rational design of highly active sgRNAs for CRISPR-Cas9–mediated gene inactivation
- (2014) John G Doench et al. NATURE BIOTECHNOLOGY
- Generation of mouse models of myeloid malignancy with combinatorial genetic lesions using CRISPR-Cas9 genome editing
- (2014) Dirk Heckl et al. NATURE BIOTECHNOLOGY
- Adenoviral vector DNA for accurate genome editing with engineered nucleases
- (2014) Maarten Holkers et al. NATURE METHODS
- Efficient genome modification by CRISPR-Cas9 nickase with minimal off-target effects
- (2014) Bin Shen et al. NATURE METHODS
- E-CRISP: fast CRISPR target site identification
- (2014) Florian Heigwer et al. NATURE METHODS
- Engineering adeno-associated viruses for clinical gene therapy
- (2014) Melissa A. Kotterman et al. NATURE REVIEWS GENETICS
- Multiplex CRISPR/Cas9-based genome engineering from a single lentiviral vector
- (2014) Ami M. Kabadi et al. NUCLEIC ACIDS RESEARCH
- Targeted inversion and reversion of the blood coagulation factor 8 gene in human iPS cells using TALENs
- (2014) C.-Y. Park et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- The new frontier of genome engineering with CRISPR-Cas9
- (2014) J. A. Doudna et al. SCIENCE
- Engineering light-inducible nuclear localization signals for precise spatiotemporal control of protein dynamics in living cells
- (2014) Dominik Niopek et al. Nature Communications
- Engineering human tumour-associated chromosomal translocations with the RNA-guided CRISPR–Cas9 system
- (2014) R. Torres et al. Nature Communications
- Targeted genomic rearrangements using CRISPR/Cas technology
- (2014) Peter S. Choi et al. Nature Communications
- Drawing a high-resolution functional map of adeno-associated virus capsid by massively parallel sequencing
- (2014) Kei Adachi et al. Nature Communications
- Adenoviral vector delivery of RNA-guided CRISPR/Cas9 nuclease complexes induces targeted mutagenesis in a diverse array of human cells
- (2014) Ignazio Maggio et al. Scientific Reports
- Simple and Rapid In Vivo Generation of Chromosomal Rearrangements using CRISPR/Cas9 Technology
- (2014) Rafael B. Blasco et al. Cell Reports
- Dynamic Imaging of Genomic Loci in Living Human Cells by an Optimized CRISPR/Cas System
- (2013) Baohui Chen et al. CELL
- Repurposing CRISPR/Cas9 for in situ functional assays
- (2013) A. Malina et al. GENES & DEVELOPMENT
- Genome-wide recessive genetic screening in mammalian cells with a lentiviral CRISPR-guide RNA library
- (2013) Hiroko Koike-Yusa et al. NATURE BIOTECHNOLOGY
- High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
- (2013) Yanfang Fu et al. NATURE BIOTECHNOLOGY
- The CRISPR Craze
- (2013) E. Pennisi SCIENCE
- Genome-Scale CRISPR-Cas9 Knockout Screening in Human Cells
- (2013) Ophir Shalem et al. SCIENCE
- Genetic Screens in Human Cells Using the CRISPR-Cas9 System
- (2013) Tim Wang et al. SCIENCE
- Harnessing the CRISPR/Cas9 system to disrupt latent HIV-1 provirus
- (2013) Hirotaka Ebina et al. Scientific Reports
- TALE nucleases: tailored genome engineering made easy
- (2012) Claudio Mussolino et al. CURRENT OPINION IN BIOTECHNOLOGY
- Development of nuclease-mediated site-specific genome modification
- (2012) Stacey E Wirt et al. CURRENT OPINION IN IMMUNOLOGY
- Retroviral Integrations in Gene Therapy Trials
- (2012) Luca Biasco et al. MOLECULAR THERAPY
- TALENs: a widely applicable technology for targeted genome editing
- (2012) J. Keith Joung et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- Optimizing Promoters for Recombinant Adeno-Associated Virus-Mediated Gene Expression in the Peripheral and Central Nervous System Using Self-Complementary Vectors
- (2011) Steven J. Gray et al. HUMAN GENE THERAPY
- Gene therapy finds its niche
- (2011) Cormac Sheridan NATURE BIOTECHNOLOGY
- Liver-specific microRNA-122 target sequences incorporated in AAV vectors efficiently inhibits transgene expression in the liver
- (2010) C Qiao et al. GENE THERAPY
- In vivo gene regulation using tetracycline-regulatable systems
- (2009) Knut Stieger et al. ADVANCED DRUG DELIVERY REVIEWS
- Directed Evolution of a Novel Adeno-associated Virus (AAV) Vector That Crosses the Seizure-compromised Blood–Brain Barrier (BBB)
- (2009) Steven J Gray et al. MOLECULAR THERAPY
- Effect of Genome Size on AAV Vector Packaging
- (2009) Zhijian Wu et al. MOLECULAR THERAPY
- Exploiting and antagonizing microRNA regulation for therapeutic and experimental applications
- (2009) Brian D. Brown et al. NATURE REVIEWS GENETICS
- Long-term correction of inhibitor-prone hemophilia B dogs treated with liver-directed AAV2-mediated factor IX gene therapy
- (2008) G. P. Niemeyer et al. BLOOD
- Viral vectors: from virology to transgene expression
- (2008) D Bouard et al. BRITISH JOURNAL OF PHARMACOLOGY
- In Vitro and In Vivo Gene Therapy Vector Evolution via Multispecies Interbreeding and Retargeting of Adeno-Associated Viruses
- (2008) D. Grimm et al. JOURNAL OF VIROLOGY
- Engineering and Selection of Shuffled AAV Genomes: A New Strategy for Producing Targeted Biological Nanoparticles
- (2008) Wuping Li et al. MOLECULAR THERAPY
- Lentiviral Vector Design for Multiple shRNA Expression and Durable HIV-1 Inhibition
- (2008) Olivier ter Brake et al. MOLECULAR THERAPY
- DNA Shuffling of Adeno-associated Virus Yields Functionally Diverse Viral Progeny
- (2008) James T Koerber et al. MOLECULAR THERAPY
Find Funding. Review Successful Grants.
Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.
ExploreAdd your recorded webinar
Do you already have a recorded webinar? Grow your audience and get more views by easily listing your recording on Peeref.
Upload Now