标题
Disruption of the Survival Motor Neuron (SMN) gene in pigs using ssDNA
作者
关键词
-
出版物
TRANSGENIC RESEARCH
Volume 20, Issue 6, Pages 1293-1304
出版商
Springer Nature
发表日期
2011-02-25
DOI
10.1007/s11248-011-9496-8
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model
- (2010) Y. Hua et al. GENES & DEVELOPMENT
- Perspectives and diagnostic considerations in spinal muscular atrophy
- (2010) Thomas W Prior GENETICS IN MEDICINE
- SAHA ameliorates the SMA phenotype in two mouse models for spinal muscular atrophy
- (2010) Markus Riessland et al. HUMAN MOLECULAR GENETICS
- Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice
- (2010) Elisa Dominguez et al. HUMAN MOLECULAR GENETICS
- Spinal muscular atrophy: mechanisms and therapeutic strategies
- (2010) C. L. Lorson et al. HUMAN MOLECULAR GENETICS
- CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy
- (2010) Marco A. Passini et al. JOURNAL OF CLINICAL INVESTIGATION
- Trans-Splicing-Mediated Improvement in a Severe Mouse Model of Spinal Muscular Atrophy
- (2010) T. H. Coady et al. JOURNAL OF NEUROSCIENCE
- Genetic therapy for spinal muscular atrophy
- (2010) Alex MacKenzie NATURE BIOTECHNOLOGY
- Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN
- (2010) Kevin D Foust et al. NATURE BIOTECHNOLOGY
- Neuromuscular defects and breathing disorders in a new mouse model of spinal muscular atrophy
- (2010) Magali Michaud et al. NEUROBIOLOGY OF DISEASE
- A short antisense oligonucleotide masking a unique intronic motif prevents skipping of a critical exon in spinal muscular atrophy
- (2010) Natalia N. Singh et al. RNA Biology
- Systemic Delivery of scAAV9 Expressing SMN Prolongs Survival in a Model of Spinal Muscular Atrophy
- (2010) C. F. Valori et al. Science Translational Medicine
- A Positive Modifier of Spinal Muscular Atrophy in the SMN2 Gene
- (2009) Thomas W. Prior et al. AMERICAN JOURNAL OF HUMAN GENETICS
- Significant Improvement in Cloning Efficiency of an Inbred Miniature Pig by Histone Deacetylase Inhibitor Treatment after Somatic Cell Nuclear Transfer1
- (2009) Jianguo Zhao et al. BIOLOGY OF REPRODUCTION
- Subcutaneous administration of TC007 reduces disease severity in an animal model of SMA
- (2009) Virginia B Mattis et al. BMC NEUROSCIENCE
- Delivery of a read-through inducing compound, TC007, lessens the severity of a spinal muscular atrophy animal model
- (2009) Virginia B. Mattis et al. HUMAN MOLECULAR GENETICS
- Effects of 2,4-diaminoquinazoline derivatives on SMN expression and phenotype in a mouse model for spinal muscular atrophy
- (2009) Matthew E.R. Butchbach et al. HUMAN MOLECULAR GENETICS
- Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy
- (2009) T. D. Baughan et al. HUMAN MOLECULAR GENETICS
- An analysis of disease severity based on SMN2 copy number in adults with spinal muscular atrophy
- (2009) Bakri Elsheikh et al. MUSCLE & NERVE
- Restoration of Full-Length SMN Promoted by Adenoviral Vectors Expressing RNA Antisense Oligonucleotides Embedded in U7 snRNAs
- (2009) Till Geib et al. PLoS One
- Tetracyclines That Promote SMN2 Exon 7 Splicing as Therapeutics for Spinal Muscular Atrophy
- (2009) M. L. Hastings et al. Science Translational Medicine
- Optimization of square-wave electroporation for transfection of porcine fetal fibroblasts
- (2009) Jason W. Ross et al. TRANSGENIC RESEARCH
- Antisense Masking of an hnRNP A1/A2 Intronic Splicing Silencer Corrects SMN2 Splicing in Transgenic Mice
- (2008) Yimin Hua et al. AMERICAN JOURNAL OF HUMAN GENETICS
- Identification and characterization of the porcine (Sus scrofa) survival motor neuron (SMN1) gene: An animal model for therapeutic studies
- (2008) Monique A. Lorson et al. DEVELOPMENTAL DYNAMICS
- Synthesis and Biological Evaluation of Novel 2,4-Diaminoquinazoline Derivatives asSMN2Promoter Activators for the Potential Treatment of Spinal Muscular Atrophy
- (2008) John Thurmond et al. JOURNAL OF MEDICINAL CHEMISTRY
- Development of a Single Vector System that Enhances Trans-Splicing of SMN2 Transcripts
- (2008) Tristan H. Coady et al. PLoS One
Publish scientific posters with Peeref
Peeref publishes scientific posters from all research disciplines. Our Diamond Open Access policy means free access to content and no publication fees for authors.
Learn MoreFind the ideal target journal for your manuscript
Explore over 38,000 international journals covering a vast array of academic fields.
Search