Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years’ treatment
出版年份 2015 全文链接
标题
Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years’ treatment
作者
关键词
Agalsidase alfa, Cardiomyopathy, Enzyme replacement therapy, Fabry disease, Left ventricular hypertrophy, Lysosomal storage disorder
出版物
Orphanet Journal of Rare Diseases
Volume 10, Issue 1, Pages -
出版商
Springer Nature
发表日期
2015-09-29
DOI
10.1186/s13023-015-0338-2
参考文献
相关参考文献
注意：仅列出部分参考文献，下载原文获取全部文献信息。- Natural course of Fabry disease and the effectiveness of enzyme replacement therapy: a systematic review and meta-analysis
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- (2009) R. Schiffmann et al. NEPHROLOGY DIALYSIS TRANSPLANTATION
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