AAV-mediated gene delivery in Dp71-null mouse model with compromised barriers

Conditional Muller Cell Ablation Causes Independent Neuronal and Vascular Pathologies in a Novel Transgenic Model

(2012) W. Shen et al.   JOURNAL OF NEUROSCIENCE

Universal Real-Time PCR for the Detection and Quantification of Adeno-Associated Virus Serotype 2-Derived Inverted Terminal Repeat Sequences

(2012) Christine Aurnhammer et al.   Human Gene Therapy Methods

Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations

(2011) Samuel G. Jacobson   ARCHIVES OF OPHTHALMOLOGY

Dystrophin Dp71: The Smallest but Multifunctional Product of the Duchenne Muscular Dystrophy Gene

(2011) Ramin Tadayoni et al.   MOLECULAR NEUROBIOLOGY

Genetic Deletion of Laminin Isoforms β2 and γ3 Induces a Reduction in Kir4.1 and Aquaporin-4 Expression and Function in the Retina

(2011) Petra G. Hirrlinger et al.   PLoS One

GFAP-Driven GFP Expression in Activated Mouse Müller Glial Cells Aligning Retinal Blood Vessels Following Intravitreal Injection of AAV2/6 Vectors

(2010) Wendy M. Aartsen et al.   PLoS One

Laminins

(2009) Madeleine Durbeej   CELL AND TISSUE RESEARCH

Changes in Adeno-Associated Virus-Mediated Gene Delivery in Retinal Degeneration

(2009) Kathleen D. Kolstad et al.   HUMAN GENE THERAPY

Inner Limiting Membrane Barriers to AAV-mediated Retinal Transduction From the Vitreous

(2009) Deniz Dalkara et al.   MOLECULAR THERAPY

A Novel Adeno-Associated Viral Variant for Efficient and Selective Intravitreal Transduction of Rat Müller Cells

(2009) Ryan R. Klimczak et al.   PLoS One

Functional Implication of Dp71 in Osmoregulation and Vascular Permeability of the Retina

(2009) Abdoulaye Sene et al.   PLoS One

Origin and turnover of ECM proteins from the inner limiting membrane and vitreous body

(2008) W Halfter et al.   EYE

Kir4.1 and AQP4 associate with Dp71- and utrophin-DAPs complexes in specific and defined microdomains of Müller retinal glial cell membrane

(2008) Patrice E. Fort et al.   GLIA

Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis

(2008) Albert M. Maguire et al.   NEW ENGLAND JOURNAL OF MEDICINE

Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

(2008) James W.B. Bainbridge et al.   NEW ENGLAND JOURNAL OF MEDICINE

Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics

(2008) A. V. Cideciyan et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA