An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease
出版年份 2018 全文链接
标题
An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease
作者
关键词
-
出版物
GENETICS IN MEDICINE
Volume -, Issue -, Pages -
出版商
Springer Nature America, Inc
发表日期
2018-09-12
DOI
10.1038/s41436-018-0270-7
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Immunomodulation to enzyme replacement therapy with tolerogenic nanoparticles containing rapamycin in a murine model of Pompe disease
- (2017) Han-Hyuk Lim et al. MOLECULAR GENETICS AND METABOLISM
- Prophylactic immune modulation in infantile Ρompe disease using low-dose methotrexate induction: A safe, inexpensive, widely accessible, and efficacious strategy
- (2016) Zoheb B. Kazi et al. MOLECULAR GENETICS AND METABOLISM
- Immune response to enzyme replacement therapies in lysosomal storage diseases and the role of immune tolerance induction
- (2016) Priya S. Kishnani et al. MOLECULAR GENETICS AND METABOLISM
- CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy
- (2015) Kathryn L. Berrier et al. GENETICS IN MEDICINE
- The expanding family of regulatory B cells
- (2015) Claudia Mauri et al. INTERNATIONAL IMMUNOLOGY
- Transient Low-Dose Methotrexate Generates B Regulatory Cells That Mediate Antigen-Specific Tolerance to Alglucosidase Alfa
- (2014) Marguerite S. Joly et al. JOURNAL OF IMMUNOLOGY
- Immune Tolerance Induced Using Plasma Exchange and Rituximab in an Infantile Pompe Disease Patient
- (2013) Federica Deodato et al. JOURNAL OF CHILD NEUROLOGY
- B-Cell Depletion and Immunomodulation before Initiation of Enzyme Replacement Therapy Blocks the Immune Response to Acid Alpha-Glucosidase in Infantile-Onset Pompe Disease
- (2013) Melissa E. Elder et al. JOURNAL OF PEDIATRICS
- Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material-Negative Classic Infantile Pompe Disease: A Step towards Improving the Efficacy of ERT
- (2013) Suhrad G. Banugaria et al. PLoS One
- Predicting cross-reactive immunological material (CRIM) status in Pompe disease using GAA mutations: Lessons learned from 10 years of clinical laboratory testing experience
- (2012) Deeksha S. Bali et al. AMERICAN JOURNAL OF MEDICAL GENETICS PART C-SEMINARS IN MEDICAL GENETICS
- The role of immune tolerance induction in restoration of the efficacy of ERT in Pompe disease
- (2012) Emanuela Lacaná et al. AMERICAN JOURNAL OF MEDICAL GENETICS PART C-SEMINARS IN MEDICAL GENETICS
- Bortezomib in the rapid reduction of high sustained antibody titers in disorders treated with therapeutic protein: lessons learned from Pompe disease
- (2012) Suhrad G. Banugaria et al. GENETICS IN MEDICINE
- Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
- (2012) Yoav H. Messinger et al. GENETICS IN MEDICINE
- Autopsy findings in late-onset Pompe disease: A case report and systematic review of the literature
- (2012) Lisa D. Hobson-Webb et al. MOLECULAR GENETICS AND METABOLISM
- Persistence of high sustained antibodies to enzyme replacement therapy despite extensive immunomodulatory therapy in an infant with Pompe disease: Need for agents to target antibody-secreting plasma cells
- (2012) Suhrad G. Banugaria et al. MOLECULAR GENETICS AND METABOLISM
- Teaching tolerance
- (2012) Leslie P. Cousens et al. Human Vaccines & Immunotherapeutics
- The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease
- (2011) Suhrad G. Banugaria et al. GENETICS IN MEDICINE
- Atypical immunologic response in a patient with CRIM-negative Pompe disease
- (2011) Mary-Alice Abbott et al. MOLECULAR GENETICS AND METABOLISM
- Immune tolerance induction to enzyme-replacement therapy by co-administration of short-term, low-dose methotrexate in a murine Pompe disease model
- (2010) A. Joseph et al. CLINICAL AND EXPERIMENTAL IMMUNOLOGY
- Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
- (2009) Marc Nicolino et al. GENETICS IN MEDICINE
- Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants
- (2009) Priya S. Kishnani et al. MOLECULAR GENETICS AND METABOLISM
- Elimination of Antibodies to Recombinant Enzyme in Pompe's Disease
- (2009) Nancy J. Mendelsohn et al. NEW ENGLAND JOURNAL OF MEDICINE
Find Funding. Review Successful Grants.
Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.
ExploreAsk a Question. Answer a Question.
Quickly pose questions to the entire community. Debate answers and get clarity on the most important issues facing researchers.
Get Started