Comparative analysis of FV vectors with human α- or β-globin gene regulatory elements for the correction of β-thalassemia

Progress in hematopoietic stem cell transplantation as allogeneic cellular gene therapy in thalassemia

(2010) Antonella Isgrò et al.   Annals of the New York Academy of Sciences

Correction of β-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patients

(2010) Emanuela Anna Roselli et al.   EMBO Molecular Medicine

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

(2010) Marina Cavazzana-Calvo et al.   NATURE

Dual transgene expression by foamy virus vectors carrying an endogenous bidirectional promoter

(2009) A Andrianaki et al.   GENE THERAPY

Foamy virus vectors: The usefulness of a perfect parasite

(2008) G Vassilopoulos et al.   GENE THERAPY

A Rapid and Quantitative Assay for Measuring Neighboring Gene Activation by Vector Proviruses

(2008) Paul C Hendrie et al.   MOLECULAR THERAPY

In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of  -thalassemia

(2008) A. Miccio et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA