rAAV2/5 gene-targeting to rods:dose-dependent efficiency and complications associated with different promoters

Gene therapy for red–green colour blindness in adult primates

(2009) Katherine Mancuso et al.   NATURE

The use of canine models of inherited retinal degeneration to test novel therapeutic approaches

(2009) William A. Beltran   VETERINARY OPHTHALMOLOGY

Operating in the Dark

(2008) András M. Komáromy   ARCHIVES OF OPHTHALMOLOGY

Targeting gene expression to cones with human cone opsin promoters in recombinant AAV

(2008) A M Komáromy et al.   GENE THERAPY

Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial

(2008) William W. Hauswirth et al.   HUMAN GENE THERAPY

Subretinal Delivery of Recombinant AAV Serotype 8 Vector in Dogs Results in Gene Transfer to Neurons in the Brain

(2008) Knut Stieger et al.   MOLECULAR THERAPY

Detection of Intact rAAV Particles up to 6 Years After Successful Gene Transfer in the Retina of Dogs and Primates

(2008) Knut Stieger et al.   MOLECULAR THERAPY

Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis

(2008) Albert M. Maguire et al.   NEW ENGLAND JOURNAL OF MEDICINE

Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

(2008) James W.B. Bainbridge et al.   NEW ENGLAND JOURNAL OF MEDICINE

Cone-specific expression using a human red opsin promoter in recombinant AAV

(2007) Qiuhong Li et al.   VISION RESEARCH

Comparative analysis of in vivo and in vitro AAV vector transduction in the neonatal mouse retina: Effects of serotype and site of administration

(2007) Ji-jing Pang et al.   VISION RESEARCH

Versatility of AAV vectors for retinal gene transfer

(2007) Enrico M. Surace et al.   VISION RESEARCH