期刊
EXPERT OPINION ON DRUG DISCOVERY
卷 13, 期 10, 页码 899-902出版社
TAYLOR & FRANCIS LTD
DOI: 10.1080/17460441.2018.1514387
关键词
Spinal muscular atrophy; motor neuron disease; gene therapy; survival motor neuron; therapy development
资金
- Wellcome Trust [106098/Z/14/Z]