Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy

The cooperative international neuromuscular research group duchenne natural history study-a longitudinal investigation in the era of glucocorticoid therapy: Design of protocol and the methods used

(2013) Craig M. McDonald et al.   MUSCLE & NERVE

24 Month Longitudinal Data in Ambulant Boys with Duchenne Muscular Dystrophy

(2013) Elena Stacy Mazzone et al.   PLoS One

A critical review of functional assessment tools for upper limbs in Duchenne muscular dystrophy

(2012) ELENA S MAZZONE et al.   DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY

International workshop on assessment of upper limb function in Duchenne Muscular Dystrophy

(2012) Eugenio Mercuri et al.   NEUROMUSCULAR DISORDERS

Innovative methods to assess upper limb strength and function in non-ambulant Duchenne patients

(2012) L. Servais et al.   NEUROMUSCULAR DISORDERS

Development and Application of Stereo Camera-Based Upper Extremity Workspace Evaluation in Patients with Neuromuscular Diseases

(2012) Gregorij Kurillo et al.   PLoS One

Moving towards meaningful measurement: Rasch analysis of the North Star Ambulatory Assessment in Duchenne muscular dystrophy

(2011) ANNA MAYHEW et al.   DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

(2011) Sebahattin Cirak et al.   LANCET

Functional changes in Duchenne muscular dystrophy: A 12-month longitudinal cohort study

(2011) E. Mazzone et al.   NEUROLOGY

Assessing upper limb function in nonambulant SMA patients: Development of a new module

(2011) Elena Mazzone et al.   NEUROMUSCULAR DISORDERS

Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy

(2011) Nathalie M. Goemans et al.   NEW ENGLAND JOURNAL OF MEDICINE

The 6-minute walk test in Duchenne/Becker muscular dystrophy: Longitudinal observations

(2010) Craig M. MCDonald et al.   MUSCLE & NERVE

North Star Ambulatory Assessment, 6-minute walk test and timed items in ambulant boys with Duchenne muscular dystrophy

(2010) Elena Mazzone et al.   NEUROMUSCULAR DISORDERS

Monitoring changes and predicting loss of ambulation in Duchenne muscular dystrophy with the Motor Function Measure

(2009) CAROLE VUILLEROT et al.   DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY

The 6-minute walk test as a new outcome measure in Duchenne muscular dystrophy

(2009) Craig M. McDonald et al.   MUSCLE & NERVE

Reliability of the North Star Ambulatory Assessment in a multicentric setting

(2009) E.S. Mazzone et al.   NEUROMUSCULAR DISORDERS

Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; Report of three expert workshops: TREAT-NMD/ENMC Workshop on outcome measures, 12th–13th May 2007, Naarden, The Netherlands; TREAT-NMD Workshop on outcome measures in experimental trials for DMD, 30th June–1st July 2007, Naarden, The Netherlands; Conjoint Institute of Myology TREAT-NMD Meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

(2008) E. Mercuri et al.   NEUROMUSCULAR DISORDERS