Long-term follow-up results after autologous haematopoietic stem cell transplantation for severe systemic sclerosis
ANNALS OF THE RHEUMATIC DISEASES (2008)
期刊
ANNALS OF THE RHEUMATIC DISEASES
卷 67, 期 1, 页码 98-104出版社
BMJ PUBLISHING GROUP
关键词
类别
作者
我是这篇论文的作者
推荐
Long-term follow-up after lymphodepleting autologous haematopoietic cell transplantation for treatment-resistant systemic lupus erythematosus
Sencer Goklemez, Sarfaraz Hasni, Frances T. Hakim, Paolo A. Muraro, Filip Pirsl, Jeremy Rose, Sarfraz Memon, Daniel F. Fowler, Seth M. Steinberg, Eva H. Baker, Sandya R. Panch, Ronald Gress, Gabor G. Illei, Peter E. Lipsky, Steven Z. Pavletic
RHEUMATOLOGY (2022)
Autologous Haematopoietic Stem Cell Transplantation and Systemic Sclerosis: Focus on Interstitial Lung Disease
Gianluca Bagnato, Antonio Giovanni Versace, Daniela La Rosa, Alberta De Gaetano, Egidio Imbalzano, Marianna Chiappalone, Carmelo Ioppolo, William Neal Roberts, Alessandra Bitto, Natasha Irrera, Alessandro Allegra, Giovanni Pioggia, Sebastiano Gangemi
CELLS (2022)
Autologous haematopoietic stem cell transplantation restores the suppressive capacity of regulatory B cells in systemic sclerosis patients
Joao R. Lima-Junior, Lucas C. M. Arruda, Maynara S. Goncalves, Juliana B. E. Dias, Daniela A. Moraes, Dimas T. Covas, Belinda P. Simoes, Maria Carolina Oliveira, Kelen C. R. Malmegrim
RHEUMATOLOGY (2021)
Autologous haematopoietic stem cell transplantation versus low-dose immunosuppression in secondary-progressive multiple sclerosis
Alice Mariottini, Giovanni Bulgarini, Benedetta Forci, Chiara Innocenti, Fabrizia Mealli, Alessandra Mattei, Chiara Ceccarelli, Anna Maria Repice, Alessandro Barilaro, Claudia Mechi, Riccardo Saccardi, Luca Massacesi
EUROPEAN JOURNAL OF NEUROLOGY (2022)
Changes on chest HRCT in systemic sclerosis-related interstitial lung disease after autologous haematopoietic stem cell transplantation
Gregory Pugnet, Antoine Petermann, Samia Collot, Philippe Otal, Pauline Lansiaux, Nassim Ait Abdallah, Gwenaelle Lorillon, Mathieu Resche-Rigon, Cecile Borel, Zora Marjanovic, Dominique Farge
RHEUMATOLOGY (2023)
Rituximab as a Treatment Option after Autologous Hematopoietic Stem Cell Transplantation in a Patient with Systemic Sclerosis
Paul Gressenberger, Philipp Jud, Gabor Kovacs, Sonja Kreuzer, Hans-Peter Brezinsek, Katharina Guetl, Viktoria Muster, Ewald Kolesnik, Albrecht Schmidt, Balazs Odler, Gabriel Adelsmayr, Peter Neumeister, Luka Brcic, Sabine Zenz, Kurt Weber, Thomas Gary, Marianne Brodmann, Winfried B. Graninger, Florentine C. Moazedi-Fuerst
JOURNAL OF PERSONALIZED MEDICINE (2021)
Autologous haematopoietic stem cell transplantation for refractory stiff-person syndrome: the UK experience
Lewis Kass-Iliyya, John A. Snowden, Alice Thorpe, Helen Jessop, Andrew D. Chantry, Ptolemaios G. Sarrigiannis, Marios Hadjivassiliou, Basil Sharrack
JOURNAL OF NEUROLOGY (2021)
Long-term follow-up demonstrates curative potential of autologous stem cell transplantation for relapsed follicular lymphoma
Robert Puckrin, Neil Chua, Kelly Chin, Anthea Peters, Peter Duggan, Mona Shafey, Jan Storek, Kareem Jamani, Carolyn Owen, Douglas Stewart
BRITISH JOURNAL OF HAEMATOLOGY (2023)
Immunosuppressive Therapy After Autologous Hematopoietic Stem Cell Transplantation in Systemic Sclerosis Patients-High Efficacy of Rituximab
Michael Gernert, Hans-Peter Tony, Matthias Froehlich, Eva Christina Schwaneck, Marc Schmalzing
FRONTIERS IN IMMUNOLOGY (2022)
Autologous haematopoietic stem cell transplantation for multiple sclerosis: a position paper and registry outline
Antonios Bayas, Achim Berthele, Norbert Blank, Peter Dreger, Simon Faissner, Manuel A. Friese, Lisa-Ann Gerdes, Oliver Martin Grauer, Vivien Haeussler, Christoph Heesen, Dietlinde Janson, Mirjam Korporal-Kuhnke, Markus Kowarik, Nikolaus Kroeger, Jan D. Luenemann, Roland Martin, Uwe Meier, Sven Meuth, Paolo Muraro, Michael Platten, Lucas Schirmer, Klarissa Hanja Stuerner, Jan Patrick Stellmann, Christof Scheid, Florian Then Bergh, Clemens Warnke, Brigitte Wildemann, Tjalf Ziemssen
THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS (2023)
Outcomes of conventionally-treated systemic sclerosis patients eligible for autologous haematopoietic stem cell transplantation
S. T. Panopoulos, M. G. Tektonidou, V-K Bournia, K. Laskari, P. P. Sfikakis
CLINICAL AND EXPERIMENTAL RHEUMATOLOGY (2021)
Improvement of microangiopathy after haematopoietic stem cell transplantation in systemic sclerosis
M. Boonstra, J. Ciaffi, D. C. Noordhoek, S. I. E. Liem, L. J. J. Beaart-van de Voorde, S. T. A. van Bijnen, T. W. J. Huizinga, M. C. Vonk, J. K. de Vries-Bouwstra
CLINICAL AND EXPERIMENTAL RHEUMATOLOGY (2022)
The current standing of autologous haematopoietic stem cell transplantation for the treatment of multiple sclerosis
A. G. Willison, T. Ruck, G. Lenz, H. P. Hartung, S. G. Meuth
JOURNAL OF NEUROLOGY (2022)
Prospective follow-up of adult long-term survivors of allogeneic haematopoietic stem cell transplantation
Anna Torrent, Christelle Ferra, Montserrat Batlle, Fatima Hidalgo, Maria-Jose Jimenez-Lorenzo, Josep-Maria Ribera
MEDICINA CLINICA (2021)
Autologous mesenchymal stem cell transplantation for spinal fusion: 10 years follow-up of a phase I/II clinical trial
Victoria Gomez-Ruiz, Juan F. Blanco, Eva M. Villaron, Helena Fidalgo, Miriam Lopez-Parra, Fermin Sanchez-Guijo
STEM CELL RESEARCH & THERAPY (2023)
Bayesian dose regimen assessment in early phase oncology incorporating pharmacokinetics and pharmacodynamics
Emma Gerard, Sarah Zohar, Hoai-Thu Thai, Christelle Lorenzato, Marie-Karelle Riviere, Moreno Ursino
BIOMETRICS (2022)
Representativeness of systemic sclerosis patients in interventional randomized trials: an analysis of the EUSTAR database
Michele Iudici, Matthias Jarlborg, Kim Lauper, Ulf Mueller-Ladner, Vanessa Smith, Yannick Allanore, Alexandra Balbir-Gurman, Andrea Doria, Paolo Airo, Ulrich A. Walker, Valeria Riccieri, Madelon C. Vonk, Armando Gabrielli, Anna-Maria Hoffmann-Vold, Gabriella Szucs, Thierry Martin, Oliver Distler, Delphine S. Courvoisier
RHEUMATOLOGY (2022)
Evidence and consensus-based recommendations for non-pharmacological treatment of fatigue, hand function loss, Raynaud's phenomenon and digital ulcers in patients with systemic sclerosis
Juliane K. Stocker, Anne A. Schouffoer, Julia Spierings, Marisca R. Schriemer, Judith Potjewijd, Lian de Pundert, Frank H. J. van den Hoogen, Maria W. G. Nijhuis-van der Sanden, J. Bart Staal, Ton Satink, Madelon C. Vonk, Cornelia H. M. van den Ende
RHEUMATOLOGY (2022)
Physical Therapy in Systemic Sclerosis: The Patient Perspective
Sophie I. E. Liem, Nina M. van Leeuwen, Thea P. M. Vliet Vlieland, Gerrie M. W. Boerrigter, Cornelia H. M. van den Ende, Lian A. J. de Pundert, Marisca R. Schriemer, Julia Spierings, Madelon C. Vonk, Jeska K. de Vries-Bouwstra
ARTHRITIS CARE & RESEARCH (2023)
Evaluation of left cardiac chamber function with cardiac magnetic resonance and association with outcome in patients with systemic sclerosis
Steele C. Butcher, Jacqueline L. Vos, Federico Fortuni, Xavier Galloo, Sophie I. E. Liem, Jeroen J. Bax, Victoria Delgado, Madelon C. Vonk, Sander van Leuven, Miranda Snoeren, Saloua El Messaoudi, Jeska K. de Vries-Bouwstra, Robin Nijveldt, Nina Ajmone Marsan
RHEUMATOLOGY (2023)
A straightforward meta-analysis approach for oncology phase I dose-finding studies
Christian Roever, Moreno Ursino, Tim Friede, Sarah Zohar
STATISTICS IN MEDICINE (2022)
Enriching single-arm clinical trials with external controls: possibilities and pitfalls
Jerome Lambert, Etienne Lengline, Raphael Porcher, Rodolphe Thiebaut, Sarah Zohar, Sylvie Chevret
BLOOD ADVANCES (2023)
Using dichotomized survival data to construct a prior distribution for a Bayesian seamless Phase II/III clinical trial
Benjamin Duputel, Nigel Stallard, Francois Montestruc, Sarah Zohar, Moreno Ursino
STATISTICAL METHODS IN MEDICAL RESEARCH (2023)
Rapid access to innovative medicinal products while ensuring relevant health technology assessment. Position of the French National Authority for Health
Antoine Vanier, Judith Fernandez, Sophie Kelley, Lise Alter, Patrick Semenzato, Corinne Alberti, Sylvie Chevret, Dominique Costagliola, Michel Cucherat, Bruno Falissard, Francois Gueyffier, Jerome Lambert, Etienne Lengline, Clara Locher, Florian Naudet, Raphael Porcher, Rodolphe Thiebaut, Muriel Vray, Sarah Zohar, Pierre Cochat, Dominique Le Guludec
BMJ EVIDENCE-BASED MEDICINE (2023)
Does the Impact of COVID-19 on Patients With Systemic Sclerosis Change Over Time?
Elisabeth Deibel, Patricia E. Carreira, Madelon Vonk, Nicoletta del Papa, Radim Becvar, Alfredo Guillen-Del-Castillo, Corrado Campochiaro, Hadi Poormoghim, Sophie Liem, Maria-Grazia Lazzaroni, Alessandro Giollo, Arsene Mekinian, Jeska de Vries-Bouwstra, Maria De Santis, Alexandra Balbir-Gurman, Carina Mihai, Giacomo De Luca, Sergey Moiseev, Elisabetta Zanatta, Rosario Foti, Simona Rednic, Christopher Denton, Maurizio Cutolo, Laura Belloli, Paolo Airo, Liudmila Garzanova, Gianluca Moroncini, Murat Inanc, Stylianos Panopoulos, Jose-Luis Tandaipan, Emmanuel Chatelus, Edoardo Rosato, Masataka Kuwana, Sule Yavuz, Juan J. Alegre-Sancho, Vanessa Smith, Gabriella Szucs, Joerg Henes, Ignasi Rodriguez-Pinto, Fabiola Atzeni, Julia Spierings, Marie-Elise Truchetet, Marcin Milchert, Daniel Brito de Araujo, Gabriela Riemekasten, Vera Bernardino, Thierry Martin, Francesco del Galdo, Alessandra Vacca, Fabian Mendoza, Oyvind Midtvedt, Giuseppe Murdaca, Tania Santiago, Veronica Codullo, Fabio Cacciapaglia, Ulrich Walker, Cathrine Brunborg, Francesca Tirelli, Yannick Allanore, Daniel E. Furst, Marco Matucci, Armando Gabrielli, Oliver Distler, Anna-Maria Hoffmann-Vold
ARTHRITIS CARE & RESEARCH (2023)
Continued Treatment with Nintedanib in Patients with Systemic Sclerosis-Associated Interstitial Lung Disease (SSc-ILD): Three-Year Data from SENSCIS-ON
Yannick Allanore, Madelon Vonk, Oliver Distler, Arata Azuma, Maureen Mayes, Alexandra James, Veronika Kohlbrenner, Margarida Alves, Dinesh Khanna, Kristin Highland
ARTHRITIS & RHEUMATOLOGY (2022)
Improvement of microangiopathy after haematopoietic stem cell transplantation in systemic sclerosis
M. Boonstra, J. Ciaffi, D. C. Noordhoek, S. I. E. Liem, L. J. J. Beaart-van de Voorde, S. T. A. van Bijnen, T. W. J. Huizinga, M. C. Vonk, J. K. de Vries-Bouwstra
CLINICAL AND EXPERIMENTAL RHEUMATOLOGY (2022)
BASELINE CHARACTERISTICS OF PATIENTS WITH IMPROVEMENT OR PROGRESSION OF SYSTEMIC SCLEROSIS-ASSOCIATED INTERSTITIAL LUNG DISEASE (SSC-ILD) DURING THE SENSCIS TRIAL
A. M. Hoffmann-Vold, E. Hachulla, A. Herrick, T. Moua, G. Riemekasten, M. Vonk, A. James, M. Alves, O. Distler
ANNALS OF THE RHEUMATIC DISEASES (2022)
Systemic sclerosis in the time of COVID-19
Anna-Maria Hoffmann-Vold, Oliver Distler, Cosimo Bruni, Christopher P. Denton, Jeska de Vries-Bouwstra, Marco Matucci Cerinic, Madelon C. Vonk, Armando Gabrielli
LANCET RHEUMATOLOGY (2022)
Personalized Dynamic Treatment Regimes in Continuous Time: A Bayesian Approach for Optimizing Clinical Decisions with Timing
William Hua, Hongyuan Mei, Sarah Zohar, Magali Giral, Yanxun Xu
BAYESIAN ANALYSIS (2022)