Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome

出版年份 2017 全文链接

标题

作者

关键词

Rett syndrome. MECP2, adeno-associated virus, gene therapy, neurodevelopmental disorder, autism, vector

出版物

Volume 5, Issue -, Pages 180-190

出版商

Elsevier BV

发表日期

2017-04-22

DOI

10.1016/j.omtm.2017.04.007

联系作者

The Peeref Institute provides free reviewer training that teaches the core competencies of the academic peer review process.

Get Started

Quickly pose questions to the entire community. Debate answers and get clarity on the most important issues facing researchers.

Get Started