A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and Restores Function in an ALS Mouse Model

出版年份 2017 全文链接

标题

作者

关键词

ALS, AAV, exon skipping, gene therapy, hSOD1

出版物

Volume 25, Issue 9, Pages 2038-2052

出版商

Elsevier BV

发表日期

2017-06-27

DOI

10.1016/j.ymthe.2017.05.017

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