Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency
出版年份 2016 全文链接
标题
Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency
作者
关键词
-
出版物
Science Translational Medicine
Volume 8, Issue 335, Pages 335ra57-335ra57
出版商
American Association for the Advancement of Science (AAAS)
发表日期
2016-04-21
DOI
10.1126/scitranslmed.aad8856
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Severe cutaneous human papillomavirus infection associated with natural killer cell deficiency following stem cell transplantation for severe combined immunodeficiency
- (2014) Qurat ul Ain Kamili et al. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY
- Enhancers Are Major Targets for Murine Leukemia Virus Vector Integration
- (2014) S. S. De Ravin et al. JOURNAL OF VIROLOGY
- Transplantation Outcomes for Severe Combined Immunodeficiency, 2000–2009
- (2014) Sung-Yun Pai et al. NEW ENGLAND JOURNAL OF MEDICINE
- A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency
- (2014) Salima Hacein-Bey-Abina et al. NEW ENGLAND JOURNAL OF MEDICINE
- Specific HIV integration sites are linked to clonal expansion and persistence of infected cells
- (2014) F. Maldarelli et al. SCIENCE
- Mobilization characteristics and strategies to improve hematopoietic progenitor cell mobilization and collection in patients with chronic granulomatous disease and severe combined immunodeficiency
- (2014) Sandhya R. Panch et al. TRANSFUSION
- Mouse Transplant Models for Evaluating the Oncogenic Risk of a Self-Inactivating XSCID Lentiviral Vector
- (2013) Sheng Zhou et al. PLoS One
- Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
- (2013) A. Aiuti et al. SCIENCE
- Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
- (2013) A. Biffi et al. SCIENCE
- Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
- (2012) F. Candotti et al. BLOOD
- Transduction of Human CD34+ Repopulating Cells with a Self-Inactivating Lentiviral Vector for SCID-X1 Produced at Clinical Scale by a Stable Cell Line
- (2012) Michael R. Greene et al. Human Gene Therapy Methods
- The host genomic environment of the provirus determines the abundance of HTLV-1-infected T-cell clones
- (2011) N. A. Gillet et al. BLOOD
- A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells
- (2010) S. Zhou et al. BLOOD
- Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
- (2010) Marina Cavazzana-Calvo et al. NATURE
- Efficacy of Gene Therapy for X-Linked Severe Combined Immunodeficiency
- (2010) Salima Hacein-Bey-Abina et al. NEW ENGLAND JOURNAL OF MEDICINE
- Differential expression of CD21 identifies developmentally and functionally distinct subsets of human transitional B cells
- (2009) S. Suryani et al. BLOOD
- Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency
- (2009) B. Neven et al. BLOOD
- Efficient construction of producer cell lines for a SIN lentiviral vector for SCID-X1 gene therapy by concatemeric array transfection
- (2009) R. E. Throm et al. BLOOD
- Hematopoietic stem cell gene therapy for adenosine deaminase deficient-SCID
- (2009) Alessandro Aiuti et al. IMMUNOLOGIC RESEARCH
- Long-term Clinical Outcome of Patients with Severe Combined Immunodeficiency Who Received Related Donor Bone Marrow Transplants without Pretransplant Chemotherapy or Post-transplant GVHD Prophylaxis
- (2009) Mary Dell Railey et al. JOURNAL OF PEDIATRICS
- Systematic and integrative analysis of large gene lists using DAVID bioinformatics resources
- (2009) Da Wei Huang et al. Nature Protocols
- Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
- (2009) Alessandro Aiuti et al. NEW ENGLAND JOURNAL OF MEDICINE
- Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients
- (2008) Steven J. Howe et al. JOURNAL OF CLINICAL INVESTIGATION
- Bioinformatics enrichment tools: paths toward the comprehensive functional analysis of large gene lists
- (2008) Da Wei Huang et al. NUCLEIC ACIDS RESEARCH
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